Long-term safety outcomes of eliglustat in patients with Gaucher disease: Prospective, multi-center, observational, post authorization safety sub-registry study
Pilar Giraldo, Isabela Batsu, Beverly Accomando, Sebastiaan J. M. Gaemers, Sefika Uslu Cil, Najat Gouyette, Maurizio Scarpa
求助PDF
{"title":"Long-term safety outcomes of eliglustat in patients with Gaucher disease: Prospective, multi-center, observational, post authorization safety sub-registry study","authors":"Pilar Giraldo, Isabela Batsu, Beverly Accomando, Sebastiaan J. M. Gaemers, Sefika Uslu Cil, Najat Gouyette, Maurizio Scarpa","doi":"10.1016/j.ymgme.2023.107844","DOIUrl":null,"url":null,"abstract":"","PeriodicalId":504050,"journal":{"name":"Molecular Genetics and Metabolism","volume":"60 27","pages":""},"PeriodicalIF":0.0000,"publicationDate":"2024-02-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":"0","resultStr":null,"platform":"Semanticscholar","paperid":null,"PeriodicalName":"Molecular Genetics and Metabolism","FirstCategoryId":"1085","ListUrlMain":"https://doi.org/10.1016/j.ymgme.2023.107844","RegionNum":0,"RegionCategory":null,"ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":null,"EPubDate":"","PubModel":"","JCR":"","JCRName":"","Score":null,"Total":0}
引用次数: 0
引用
批量引用