Hali Sai, Bethany Ollington, Farah O. Rezek, Niuzheng Chai, Amelia Lane, Tassos Georgiadis, James Bainbridge, Michel Michaelides, Almudena Sacristán-Reviriego, P. Perdigão, Amy Leung, J. van der Spuy
{"title":"Effective AAV-mediated gene replacement therapy in retinal organoids modelling AIPL1-associated LCA4","authors":"Hali Sai, Bethany Ollington, Farah O. Rezek, Niuzheng Chai, Amelia Lane, Tassos Georgiadis, James Bainbridge, Michel Michaelides, Almudena Sacristán-Reviriego, P. Perdigão, Amy Leung, J. van der Spuy","doi":"10.1016/j.omtn.2024.102148","DOIUrl":null,"url":null,"abstract":"","PeriodicalId":503104,"journal":{"name":"Molecular Therapy - Nucleic Acids","volume":"33 4","pages":""},"PeriodicalIF":0.0000,"publicationDate":"2024-02-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":"0","resultStr":null,"platform":"Semanticscholar","paperid":null,"PeriodicalName":"Molecular Therapy - Nucleic Acids","FirstCategoryId":"1085","ListUrlMain":"https://doi.org/10.1016/j.omtn.2024.102148","RegionNum":0,"RegionCategory":null,"ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":null,"EPubDate":"","PubModel":"","JCR":"","JCRName":"","Score":null,"Total":0}