B. den Hollander, M. M. Brands, I. Nijhuis, Lous J A E Doude van Troostwijk, P. van Essen, G. H. Hofsteenge, Bart G. Koot, Annelieke R. Müller, Laura Tseng, E. Stroes, P. M. van de Ven, A. Wiegman, C. D. van Karnebeek
{"title":"Breaking the chains of lipoprotein lipase deficiency: A pediatric perspective on the efficacy and safety of Volanesorsen","authors":"B. den Hollander, M. M. Brands, I. Nijhuis, Lous J A E Doude van Troostwijk, P. van Essen, G. H. Hofsteenge, Bart G. Koot, Annelieke R. Müller, Laura Tseng, E. Stroes, P. M. van de Ven, A. Wiegman, C. D. van Karnebeek","doi":"10.1016/j.ymgme.2024.108347","DOIUrl":null,"url":null,"abstract":"","PeriodicalId":504050,"journal":{"name":"Molecular Genetics and Metabolism","volume":"107 10","pages":""},"PeriodicalIF":0.0000,"publicationDate":"2024-02-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":"0","resultStr":null,"platform":"Semanticscholar","paperid":null,"PeriodicalName":"Molecular Genetics and Metabolism","FirstCategoryId":"1085","ListUrlMain":"https://doi.org/10.1016/j.ymgme.2024.108347","RegionNum":0,"RegionCategory":null,"ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":null,"EPubDate":"","PubModel":"","JCR":"","JCRName":"","Score":null,"Total":0}