Effect size analysis of cipaglucosidase alfa plus miglustat versus alglucosidase alfa in ERT-experienced adults with late-onset Pompe disease in PROPEL
T. Mozaffar, D. Bratkovic, B. Byrne, K. Claeys, Jordi Díaz-Manera, M. Dimachkie, Priya S. Kishnani, H. Kushlaf, Mark E. Roberts, Antonio Toscano, J. Castelli, F. Holdbrook, Sheela Sitaraman Das, Y. Wasfi, Benedikt Schoser
{"title":"Effect size analysis of cipaglucosidase alfa plus miglustat versus alglucosidase alfa in ERT-experienced adults with late-onset Pompe disease in PROPEL","authors":"T. Mozaffar, D. Bratkovic, B. Byrne, K. Claeys, Jordi Díaz-Manera, M. Dimachkie, Priya S. Kishnani, H. Kushlaf, Mark E. Roberts, Antonio Toscano, J. Castelli, F. Holdbrook, Sheela Sitaraman Das, Y. Wasfi, Benedikt Schoser","doi":"10.1016/j.ymgme.2023.107971","DOIUrl":null,"url":null,"abstract":"","PeriodicalId":504050,"journal":{"name":"Molecular Genetics and Metabolism","volume":"14 8","pages":""},"PeriodicalIF":0.0000,"publicationDate":"2024-02-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":"0","resultStr":null,"platform":"Semanticscholar","paperid":null,"PeriodicalName":"Molecular Genetics and Metabolism","FirstCategoryId":"1085","ListUrlMain":"https://doi.org/10.1016/j.ymgme.2023.107971","RegionNum":0,"RegionCategory":null,"ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":null,"EPubDate":"","PubModel":"","JCR":"","JCRName":"","Score":null,"Total":0}
京公网安备 11010802042870号
京ICP备2023020795号-1
分享
求助内容：
应助结果提醒方式：
扫码关注我们
