M021 (rhGAA) has a unique glycosylation profile which enables more efficient glycogen reduction and may allow for alternative Pompe ERT dosing strategies
Kylie Gray, Michael DiGruccio, Jonathan Roberts, Vaughn Weaver, Riley Marcinczyk, Linda Lyons, Udayanga S Wanninayake, Shou-nian Liu, N. Brignol, Osman Sheikh, Clarissa Booth, Steven B. Ortmeier, Katherine White, Hung Do, Russell Gotshall
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