{"title":"停止CRISPR基因治疗镰状细胞病可改善症状。","authors":"Thiago Carvalho","doi":"10.1038/d41591-023-00088-6","DOIUrl":null,"url":null,"abstract":"Nature Medicine explores the latest translation and clinical research news, with results from a clinical trial of Novartis'' discontinued gene therapy to restore fetal hemoglobin. Nature Medicine explores the latest translation and clinical research news, with results from a clinical trial of Novartis'' discontinued gene therapy to restore fetal hemoglobin.","PeriodicalId":19037,"journal":{"name":"Nature Medicine","volume":"29 11","pages":"2669-2670"},"PeriodicalIF":58.7000,"publicationDate":"2023-10-02","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":"0","resultStr":"{\"title\":\"Discontinued CRISPR gene therapy for sickle-cell disease improves symptoms\",\"authors\":\"Thiago Carvalho\",\"doi\":\"10.1038/d41591-023-00088-6\",\"DOIUrl\":null,\"url\":null,\"abstract\":\"Nature Medicine explores the latest translation and clinical research news, with results from a clinical trial of Novartis'' discontinued gene therapy to restore fetal hemoglobin. Nature Medicine explores the latest translation and clinical research news, with results from a clinical trial of Novartis'' discontinued gene therapy to restore fetal hemoglobin.\",\"PeriodicalId\":19037,\"journal\":{\"name\":\"Nature Medicine\",\"volume\":\"29 11\",\"pages\":\"2669-2670\"},\"PeriodicalIF\":58.7000,\"publicationDate\":\"2023-10-02\",\"publicationTypes\":\"Journal Article\",\"fieldsOfStudy\":null,\"isOpenAccess\":false,\"openAccessPdf\":\"\",\"citationCount\":\"0\",\"resultStr\":null,\"platform\":\"Semanticscholar\",\"paperid\":null,\"PeriodicalName\":\"Nature Medicine\",\"FirstCategoryId\":\"3\",\"ListUrlMain\":\"https://www.nature.com/articles/d41591-023-00088-6\",\"RegionNum\":1,\"RegionCategory\":\"医学\",\"ArticlePicture\":[],\"TitleCN\":null,\"AbstractTextCN\":null,\"PMCID\":null,\"EPubDate\":\"\",\"PubModel\":\"\",\"JCR\":\"Q1\",\"JCRName\":\"BIOCHEMISTRY & MOLECULAR BIOLOGY\",\"Score\":null,\"Total\":0}","platform":"Semanticscholar","paperid":null,"PeriodicalName":"Nature Medicine","FirstCategoryId":"3","ListUrlMain":"https://www.nature.com/articles/d41591-023-00088-6","RegionNum":1,"RegionCategory":"医学","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":null,"EPubDate":"","PubModel":"","JCR":"Q1","JCRName":"BIOCHEMISTRY & MOLECULAR BIOLOGY","Score":null,"Total":0}
Discontinued CRISPR gene therapy for sickle-cell disease improves symptoms
Nature Medicine explores the latest translation and clinical research news, with results from a clinical trial of Novartis'' discontinued gene therapy to restore fetal hemoglobin. Nature Medicine explores the latest translation and clinical research news, with results from a clinical trial of Novartis'' discontinued gene therapy to restore fetal hemoglobin.
期刊介绍：
Nature Medicine is a monthly journal publishing original peer-reviewed research in all areas of medicine. The publication focuses on originality, timeliness, interdisciplinary interest, and the impact on improving human health. In addition to research articles, Nature Medicine also publishes commissioned content such as News, Reviews, and Perspectives. This content aims to provide context for the latest advances in translational and clinical research, reaching a wide audience of M.D. and Ph.D. readers. All editorial decisions for the journal are made by a team of full-time professional editors.
Nature Medicine consider all types of clinical research, including:
-Case-reports and small case series
-Clinical trials, whether phase 1, 2, 3 or 4
-Observational studies
-Meta-analyses
-Biomarker studies
-Public and global health studies
Nature Medicine is also committed to facilitating communication between translational and clinical researchers. As such, we consider “hybrid” studies with preclinical and translational findings reported alongside data from clinical studies.
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