A. Bhattacharyya, Effenberger Kerstin, C. Trotta, J. Narasimhan, Wencheng Li, G. WollMatthew, B. JaniMinakshi, N. Risher, Shirley Yeh, Yaofeng Cheng, N. Sydorenko, M. Weetall, A. Southwell, Michael R. Hayden, J. Colacino, S. Peltz
{"title":"I01 Orally bioavailable small molecule splicing modifiers with systemic and even htt-lowering activity in vitro and in vivo","authors":"A. Bhattacharyya, Effenberger Kerstin, C. Trotta, J. Narasimhan, Wencheng Li, G. WollMatthew, B. JaniMinakshi, N. Risher, Shirley Yeh, Yaofeng Cheng, N. Sydorenko, M. Weetall, A. Southwell, Michael R. Hayden, J. Colacino, S. Peltz","doi":"10.1136/jnnp-2021-ehdn.115","DOIUrl":null,"url":null,"abstract":"","PeriodicalId":444837,"journal":{"name":"I: Experimental therapeutics – preclinical","volume":"69 1","pages":"0"},"PeriodicalIF":0.0000,"publicationDate":"2021-09-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":"0","resultStr":null,"platform":"Semanticscholar","paperid":null,"PeriodicalName":"I: Experimental therapeutics – preclinical","FirstCategoryId":"1085","ListUrlMain":"https://doi.org/10.1136/jnnp-2021-ehdn.115","RegionNum":0,"RegionCategory":null,"ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":null,"EPubDate":"","PubModel":"","JCR":"","JCRName":"","Score":null,"Total":0}