I04 Aav5-mihtt gene therapy mediates sustained mutant huntingtin lowering in brain and cerebrospinal fluid of Huntington disease minipigs up to 4 years
L. V. D. Bent, C. Brouwers, Robin Pocornie, A. Stam, Steffi Jonk, J. Klíma, Š. Juhás, J. Motlík, M. Evers, Zdenka Ellederovaé, A. Vallès
{"title":"I04 Aav5-mihtt gene therapy mediates sustained mutant huntingtin lowering in brain and cerebrospinal fluid of Huntington disease minipigs up to 4 years","authors":"L. V. D. Bent, C. Brouwers, Robin Pocornie, A. Stam, Steffi Jonk, J. Klíma, Š. Juhás, J. Motlík, M. Evers, Zdenka Ellederovaé, A. Vallès","doi":"10.1136/jnnp-2022-ehdn.230","DOIUrl":null,"url":null,"abstract":"","PeriodicalId":444837,"journal":{"name":"I: Experimental therapeutics – preclinical","volume":"10 1","pages":"0"},"PeriodicalIF":0.0000,"publicationDate":"2022-09-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":"0","resultStr":null,"platform":"Semanticscholar","paperid":null,"PeriodicalName":"I: Experimental therapeutics – preclinical","FirstCategoryId":"1085","ListUrlMain":"https://doi.org/10.1136/jnnp-2022-ehdn.230","RegionNum":0,"RegionCategory":null,"ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":null,"EPubDate":"","PubModel":"","JCR":"","JCRName":"","Score":null,"Total":0}