A. Rashnonejad, Gholamhossein Amini Chermahini, Cumhur Gündüz, H. Onay, A. Aykut, B. Durmaz, M. Baka, Q. Su, G. Gao, F. Özkınay
{"title":"Fetal Gene Therapy Using a Single Injection of Recombinant AAV9 Rescued SMA Phenotype in Mice.","authors":"A. Rashnonejad, Gholamhossein Amini Chermahini, Cumhur Gündüz, H. Onay, A. Aykut, B. Durmaz, M. Baka, Q. Su, G. Gao, F. Özkınay","doi":"10.1016/j.ymthe.2019.08.017","DOIUrl":null,"url":null,"abstract":"","PeriodicalId":19039,"journal":{"name":"Molecular Therapy: the Journal of the American Society of Gene Therapy","volume":"51 1","pages":""},"PeriodicalIF":0.0000,"publicationDate":"2019-12-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":"23","resultStr":null,"platform":"Semanticscholar","paperid":null,"PeriodicalName":"Molecular Therapy: the Journal of the American Society of Gene Therapy","FirstCategoryId":"1085","ListUrlMain":"https://doi.org/10.1016/j.ymthe.2019.08.017","RegionNum":0,"RegionCategory":null,"ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":null,"EPubDate":"","PubModel":"","JCR":"","JCRName":"","Score":null,"Total":0}