Investor Outlook: Solving Gene Therapy Pricing…with a Cures Voucher?

SchimmerJoshua, BreazzanoSteven
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引用次数: 4

Abstract

Gene therapy reimbursement continues to be an intense topic of discussion in the field given the unique and durable benefits from a single administration and generally small patient populations against a reimbursement framework that is not optimized for such “cures” or long-lived benefits. As more gene therapy programs enter the market and late-stage development, it is increasingly important for the field to define a reimbursement model that works for all stakeholders in order to encourage the next wave of innovation. To add to the discussion around new payment models and potential solutions, we propose a flexible voucher system that takes advantage of existing infrastructure, precedent, and regulatory frameworks.
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投资者展望:用治疗券解决基因治疗定价问题?
基因治疗报销仍然是该领域讨论的一个激烈话题,因为单次给药的独特和持久的好处,以及通常较小的患者群体,而报销框架并没有针对这种“治愈”或长期的好处进行优化。随着越来越多的基因治疗项目进入市场和后期开发阶段,为鼓励下一波创新,该领域定义一个适用于所有利益相关者的报销模式变得越来越重要。为了增加对新的支付模式和潜在解决方案的讨论,我们提出了一个灵活的凭证系统,利用现有的基础设施、先例和监管框架。
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来源期刊
Human Gene Therapy Clinical Development
Human Gene Therapy Clinical Development CRITICAL CARE MEDICINEMEDICINE, RESEARCH &-MEDICINE, RESEARCH & EXPERIMENTAL
CiteScore
7.20
自引率
0.00%
发文量
0
期刊介绍: Human Gene Therapy (HGT) is the premier, multidisciplinary journal covering all aspects of gene therapy. The Journal publishes important advances in DNA, RNA, cell and immune therapies, validating the latest advances in research and new technologies.
期刊最新文献
MiR-625-5p inhibits cardiac hypertrophy through targeting STAT3 and CaMKII. Circular RNA circVAPA promotes cell proliferation in hepatocellular carcinoma. Gene Therapy Briefs. The influence of murine genetic background in AAV transduction of the mouse brain. Inhibition of miR-203 ameliorates osteoarthritis cartilage degradation in the postmenopausal rat model: involvement of estrogen receptor α.
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