小儿重症肌无力

E. Tiongson
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引用次数: 0

摘要

摘要:小儿重症肌无力(MG)是一种相对罕见但非常可治疗的疾病。与成人相比,儿童重症肌无力的预后有利于最小表现状态(MMS)或缓解。仅眼部表现更为常见,但也有严重难治性全身性MG表现。观察性检查是临床诊断和随访儿童MG患者的关键。治疗选择受到副作用和生长因素的限制,以及在儿科人群中缺乏批准的MG药物。小儿MG应考虑多学科治疗,类似于其他神经肌肉疾病的专科护理设置。
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Pediatric Myasthenia Gravis
Abstract: Pediatric myasthenia gravis (MG) is a relatively rare, but very treatable condition. Prognosis in pediatric myasthenia gravis is favorable for minimal manifestation status (MMS) or remission when compared to adults. Ocular only presentations are more common, though severe refractory generalized MG presentations also occur. An observational examination is key to the diagnosis and follow-up of pediatric MG patients in the clinic setting. Treatment options are limited by side effect and growth considerations, as well as lack of approved MG medications in the pediatric population. Multidisciplinary care should be considered for pediatric MG, similar to other neuromuscular conditions seen in specialty care settings.
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