W. Miesbach, M. Recht, N. Key, K. Sivamurthy, E. P. Monahan, W. S. Pipe
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Durability of Factor IX activity and bleeding rate in people with severe or moderately severe haemophilia B after long-term follow-up in the phase 1/2 Study of AMT-060, and phase 2b and phase 3 studies of etranacogene dezaparvovec (AMT-061)