I01口服小分子剪接修饰剂，具有全身甚至体外和体内降低温度的活性

{"title":"I01口服小分子剪接修饰剂，具有全身甚至体外和体内降低温度的活性","authors":"A. Bhattacharyya, Effenberger Kerstin, C. Trotta, J. Narasimhan, Wencheng Li, G. WollMatthew, B. JaniMinakshi, N. Risher, Shirley Yeh, Yaofeng Cheng, N. Sydorenko, M. Weetall, A. Southwell, Michael R. Hayden, J. Colacino, S. Peltz","doi":"10.1136/jnnp-2021-ehdn.115","DOIUrl":null,"url":null,"abstract":"","PeriodicalId":444837,"journal":{"name":"I: Experimental therapeutics – preclinical","volume":"69 1","pages":"0"},"PeriodicalIF":0.0000,"publicationDate":"2021-09-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":"0","resultStr":"{\"title\":\"I01 Orally bioavailable small molecule splicing modifiers with systemic and even htt-lowering activity in vitro and in vivo\",\"authors\":\"A. Bhattacharyya, Effenberger Kerstin, C. Trotta, J. Narasimhan, Wencheng Li, G. WollMatthew, B. JaniMinakshi, N. Risher, Shirley Yeh, Yaofeng Cheng, N. Sydorenko, M. Weetall, A. Southwell, Michael R. Hayden, J. Colacino, S. Peltz\",\"doi\":\"10.1136/jnnp-2021-ehdn.115\",\"DOIUrl\":null,\"url\":null,\"abstract\":\"\",\"PeriodicalId\":444837,\"journal\":{\"name\":\"I: Experimental therapeutics – preclinical\",\"volume\":\"69 1\",\"pages\":\"0\"},\"PeriodicalIF\":0.0000,\"publicationDate\":\"2021-09-01\",\"publicationTypes\":\"Journal Article\",\"fieldsOfStudy\":null,\"isOpenAccess\":false,\"openAccessPdf\":\"\",\"citationCount\":\"0\",\"resultStr\":null,\"platform\":\"Semanticscholar\",\"paperid\":null,\"PeriodicalName\":\"I: Experimental therapeutics – preclinical\",\"FirstCategoryId\":\"1085\",\"ListUrlMain\":\"https://doi.org/10.1136/jnnp-2021-ehdn.115\",\"RegionNum\":0,\"RegionCategory\":null,\"ArticlePicture\":[],\"TitleCN\":null,\"AbstractTextCN\":null,\"PMCID\":null,\"EPubDate\":\"\",\"PubModel\":\"\",\"JCR\":\"\",\"JCRName\":\"\",\"Score\":null,\"Total\":0}","platform":"Semanticscholar","paperid":null,"PeriodicalName":"I: Experimental therapeutics – preclinical","FirstCategoryId":"1085","ListUrlMain":"https://doi.org/10.1136/jnnp-2021-ehdn.115","RegionNum":0,"RegionCategory":null,"ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":null,"EPubDate":"","PubModel":"","JCR":"","JCRName":"","Score":null,"Total":0}