FollowME 法布里开拓者登记：接受米格司他治疗至少三年的一组患者的肾脏疗效

{"title":"FollowME 法布里开拓者登记：接受米格司他治疗至少三年的一组患者的肾脏疗效","authors":"Michael L. West, Derralynn Hughes, G. Sunder-Plassmann, Ana Jovanovic, Eva Brand, Daniel G. Bichet, Antonio Pisani, Albina Nowak, Roser Torra, Aneal Khan, Olga Azevedo, Anna Lehman, A. Linhart, Jasmine Rutecki, J. Giuliano, E. Krusinska, Peter Nordbeck","doi":"10.1016/j.ymgme.2023.108078","DOIUrl":null,"url":null,"abstract":"","PeriodicalId":504050,"journal":{"name":"Molecular Genetics and Metabolism","volume":"18 4","pages":""},"PeriodicalIF":0.0000,"publicationDate":"2024-02-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":"0","resultStr":"{\"title\":\"FollowME Fabry Pathfinders Registry: Renal effectiveness in a cohort of patients on migalastat treatment for at least three years\",\"authors\":\"Michael L. West, Derralynn Hughes, G. Sunder-Plassmann, Ana Jovanovic, Eva Brand, Daniel G. Bichet, Antonio Pisani, Albina Nowak, Roser Torra, Aneal Khan, Olga Azevedo, Anna Lehman, A. Linhart, Jasmine Rutecki, J. Giuliano, E. Krusinska, Peter Nordbeck\",\"doi\":\"10.1016/j.ymgme.2023.108078\",\"DOIUrl\":null,\"url\":null,\"abstract\":\"\",\"PeriodicalId\":504050,\"journal\":{\"name\":\"Molecular Genetics and Metabolism\",\"volume\":\"18 4\",\"pages\":\"\"},\"PeriodicalIF\":0.0000,\"publicationDate\":\"2024-02-01\",\"publicationTypes\":\"Journal Article\",\"fieldsOfStudy\":null,\"isOpenAccess\":false,\"openAccessPdf\":\"\",\"citationCount\":\"0\",\"resultStr\":null,\"platform\":\"Semanticscholar\",\"paperid\":null,\"PeriodicalName\":\"Molecular Genetics and Metabolism\",\"FirstCategoryId\":\"1085\",\"ListUrlMain\":\"https://doi.org/10.1016/j.ymgme.2023.108078\",\"RegionNum\":0,\"RegionCategory\":null,\"ArticlePicture\":[],\"TitleCN\":null,\"AbstractTextCN\":null,\"PMCID\":null,\"EPubDate\":\"\",\"PubModel\":\"\",\"JCR\":\"\",\"JCRName\":\"\",\"Score\":null,\"Total\":0}","platform":"Semanticscholar","paperid":null,"PeriodicalName":"Molecular Genetics and Metabolism","FirstCategoryId":"1085","ListUrlMain":"https://doi.org/10.1016/j.ymgme.2023.108078","RegionNum":0,"RegionCategory":null,"ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":null,"EPubDate":"","PubModel":"","JCR":"","JCRName":"","Score":null,"Total":0}