腺嘌呤碱基编辑器纠正了 hiPSC 和肾脏器官组织中的 ADPKD 点突变

Jingwen Wang, Yanling Qiu, Lei Zhang, Xinyao Zhou, Sihui Hu, Qianyi Liu, Sisi Yin, Zehong Su, Simiao Liu, Haiying Liu, Xueqing Wu, Junjiu Huang
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Adenine base editor corrected ADPKD point mutations in hiPSCs and kidney organoids
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