Anna Lokchine, Anne Bergougnoux, Nadège Servant, Linda Akloul, Erika Launay, Laura Mary, Laurence Cluzeau, Mathieu Philippe, Mathilde Domin-Bernhard, Solène Duros, Sylvie Odent, Elena Tucker, Françoise Paris, Marc-Antoine Belaud-Rotureau, Sylvie Jaillard
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引用次数: 0
摘要
促卵泡激素(FSH)是一种与人类生育有关的关键垂体促性腺激素,对卵泡生成和新前叶卵泡的募集至关重要。其受体FSHR的变异可导致多种生殖表型,包括卵巢过度刺激综合征(OHSS)和卵巢早衰(POI)。本研究报告了一例与 FSHR 相关的卵巢功能不全的新病例,患者原发性闭经、AMH 水平异常和青春期延迟。基因检测发现了两个 FSHR 基因内复合杂合缺失。具体来说,该患者遗传了一个跨越 5-10 号外显子的母源性缺失和一个涉及 3-6 号外显子的父源性缺失。通过染色体微阵列分析(CMA)、外显子组测序、长程 PCR 和 Sanger 测序,我们确定了断点的特征,并确认了复合杂合缺失。研究结果表明,两个 FSHR 等位基因完全丧失功能,导致了患者的 POI 表型。该病例强调了 FSHR 相关疾病中基因型与表型相关性的复杂性,以及 CNV 在 POI 表型中的作用。尽管这些事件非常罕见,但我们的研究结果主张将 CNV 检测纳入 POI 的诊断工作中,以确保准确诊断和更好地管理患者。
Identification and Characterization of Novel FSHR Copy Number Variations Causing Premature Ovarian Insufficiency.
Follicle stimulating hormone (FSH) is a key pituitary gonadotropic hormone implicated in human fertility and is crucial for folliculogenesis and recruitment of new antral follicles. Variations in its receptor, FSHR, can lead to diverse reproductive phenotypes including ovarian hyperstimulation syndrome (OHSS) and premature ovarian insufficiency (POI). This study reports a novel case of FSHR-related ovarian insufficiency in a patient with primary amenorrhea, subnormal AMH levels, and delayed puberty. Genetic exploration revealed two compound heterozygous intragenic deletions of FSHR. Specifically, the patient inherited a maternally derived deletion spanning exons 5-10 and a paternally derived deletion involving exons 3-6. Through chromosomal microarray analysis (CMA), exome sequencing, long-range PCR, and Sanger sequencing, we characterized the breakpoints and confirmed the compound heterozygous deletions. The findings reveal a complete loss of function of both FSHR alleles, contributing to the patient's POI phenotype. This case emphasizes the complexity of genotype-phenotype correlations in FSHR-related disorders and the role of CNVs in POI phenotypes. Although these events are rare, our results advocate for the inclusion of CNV detection in the diagnostic workup of POI to ensure accurate diagnosis and better patient management.
期刊介绍:
The American Journal of Medical Genetics - Part A (AJMG) gives you continuous coverage of all biological and medical aspects of genetic disorders and birth defects, as well as in-depth documentation of phenotype analysis within the current context of genotype/phenotype correlations. In addition to Part A , AJMG also publishes two other parts:
Part B: Neuropsychiatric Genetics , covering experimental and clinical investigations of the genetic mechanisms underlying neurologic and psychiatric disorders.
Part C: Seminars in Medical Genetics , guest-edited collections of thematic reviews of topical interest to the readership of AJMG .