管理严重同型蛋白 c 缺乏症的挑战:一份病例报告。

IF 1.2 4区 医学 Q4 HEMATOLOGY Blood Coagulation & Fibrinolysis Pub Date : 2024-11-05 DOI:10.1097/MBC.0000000000001332
Eman Almatter, Sondus Alsharidah, Mona Bourhama, Maha Bourusly, Mohamad Adel Obaid
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引用次数: 0

摘要

蛋白 C 缺乏症是一种罕见的常染色体隐性遗传疾病,与血栓栓塞并发症的高风险有关。本病例报告描述了一名 23 岁女性在婴儿期就被诊断出患有严重的同型 C 蛋白缺乏症,在治疗过程中面临的挑战。她的病史包括误诊为蜂窝组织炎、反复血栓形成和一只眼睛永久性失明。实验室检查确诊她患有严重的蛋白 C 缺乏症。治疗方案包括新鲜冰冻血浆(FFP)、浓缩蛋白 C、华法林和肝素,但由于反复出现血栓和对 FFP 过敏,治疗一直面临挑战。该病例凸显了严重蛋白 C 缺乏症诊断和治疗所面临的挑战。尽管目前的治疗方案可以部分控制病情,但进一步的研究对于开发更安全、更有效的疗法以改善患者的长期预后至关重要。
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Challenges in managing severe homozygous protein c deficiency: a case report.

Protein C deficiency is a rare autosomal recessive disorder associated with a high risk of thromboembolic complications. This case report describes the challenges in managing a 23-year-old woman with severe homozygous protein C type 1 deficiency diagnosed since early infancy. Her medical history included misdiagnosed cellulitis, recurrent thrombosis, and permanent vision loss in one eye. The laboratory workup confirmed a diagnosis of severe protein C deficiency. Management involved a combination of fresh frozen plasma (FFP), protein C concentrate, warfarin, and heparin, with ongoing challenges due to recurrent thrombosis and anaphylaxis to FFP. This case highlights the challenges in the diagnosis and management of severe protein C deficiency. Although current treatment options provide partial control, further research is crucial to develop safer and more effective therapies to improve long-term outcomes for affected patients.

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来源期刊
CiteScore
1.90
自引率
0.00%
发文量
111
审稿时长
4-8 weeks
期刊介绍: Blood Coagulation & Fibrinolysis is an international fully refereed journal that features review and original research articles on all clinical, laboratory and experimental aspects of haemostasis and thrombosis. The journal is devoted to publishing significant developments worldwide in the field of blood coagulation, fibrinolysis, thrombosis, platelets and the kininogen-kinin system, as well as dealing with those aspects of blood rheology relevant to haemostasis and the effects of drugs on haemostatic components
期刊最新文献
Variation among venous thromboembolism risk assessment tools for postcesarean patients: a retrospective cohort study. Is the combination of two automated rapid assays for diagnosis of heparin-induced thrombocytopenia necessary? Challenges in managing severe homozygous protein c deficiency: a case report. A novel SERPINC1 c.119G>A (p.Cys40Tyr) mutation with variable clinical expression in an Indian family. A novel γ-chain mutation p.Asp318His in a Chinese family with dysfibrinogenemia.
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