Joecelyn Kirani Tan, Wireko Andrew Awuah, Arjun Ahluwalia, Vivek Sanker, Adam Ben-Jaafar, Pearl Ohenewaa Tenkorang, Nicholas Aderinto, Aashna Mehta, Kwadwo Darko, Muhammad Hamza Shah, Sakshi Roy, Toufik Abdul-Rahman, Oday Atallah
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引用次数: 0
摘要
全外显子组测序(WES)是一项开创性技术,已成为神经内科和神经外科的关键技术,可全面阐明各种神经系统疾病的基因状况。这种变革性的方法集中于 DNA 的外显子部分(约占人类基因组的 1%),从而促进了快速高效的测序过程。通过揭示罕见变异和新型突变,并深入了解其遗传复杂性,WES 在促进我们对神经退行性疾病、神经肿瘤学、脑血管疾病和癫痫的了解方面发挥了重要作用。在实现这一目标的同时,还保持了可观的诊断率,从而为这些疾病的病理生理学和个性化治疗提供了新的视角。与其他基因测序方法相比,使用 WES 有许多优点,包括成本效益高、减少偶然发现、简化分析和解释过程以及降低计算需求。然而,尽管WES具有诸多优点,但也存在一些挑战,例如对意义不明的变异的解释、成本考虑以及在资源有限的环境中的可及性有限。此外,还提出了伦理、法律和社会方面的问题,特别是在偶然发现和病人同意的情况下。展望未来,WES 与其他基于全息图学的方法的整合将有助于通过其在预测模型和靶向治疗策略开发中的意义彻底改变个性化医学领域,标志着向更有效和以临床为导向的解决方案迈出了一大步。
Genes to therapy: a comprehensive literature review of whole-exome sequencing in neurology and neurosurgery.
Whole-exome sequencing (WES), a ground-breaking technology, has emerged as a linchpin in neurology and neurosurgery, offering a comprehensive elucidation of the genetic landscape of various neurological disorders. This transformative methodology concentrates on the exonic portions of DNA, which constitute approximately 1% of the human genome, thus facilitating an expedited and efficient sequencing process. WES has been instrumental in advancing our understanding of neurodegenerative diseases, neuro-oncology, cerebrovascular disorders, and epilepsy by revealing rare variants and novel mutations and providing intricate insights into their genetic complexities. This has been achieved while maintaining a substantial diagnostic yield, thereby offering novel perspectives on the pathophysiology and personalized management of these conditions. The utilization of WES boasts several advantages over alternative genetic sequencing methodologies, including cost-effectiveness, reduced incidental findings, simplified analysis and interpretation process, and reduced computational demands. However, despite its benefits, there are challenges, such as the interpretation of variants of unknown significance, cost considerations, and limited accessibility in resource-constrained settings. Additionally, ethical, legal, and social concerns are raised, particularly in the context of incidental findings and patient consent. As we look to the future, the integration of WES with other omics-based approaches could help revolutionize the field of personalized medicine through its implications in predictive models and the development of targeted therapeutic strategies, marking a significant stride toward more effective and clinically oriented solutions.
期刊介绍:
European Journal of Medical Research publishes translational and clinical research of international interest across all medical disciplines, enabling clinicians and other researchers to learn about developments and innovations within these disciplines and across the boundaries between disciplines. The journal publishes high quality research and reviews and aims to ensure that the results of all well-conducted research are published, regardless of their outcome.