Lumasiran治疗晚期原发性1型高草酸尿的疗效和安全性:3期illumate - c试验的24个月随访
Anne-Laure Sellier-Leclerc MD , Daniella Magen MD , Hadas Shasha-Lavsky MD , Eva Simkova MD , Arnaud Devresse MD, PhD , Fitsum Guebre-Egziabher MD, PhD , Mini Michael MD , John C. Lieske MD , Yaacov Frishberg MD , Sevcan A. Bakkaloglu MD , Chebl Mourani MD , Rola Saqan MD , Richard Singer MBChB , Isabella Guzzo MD , Nune Makarova MD, MPH , Richard Willey MS , Cristin Kaspar MD , John M. Gansner MD, PhD , Jaap W. Groothoff MD, PhD
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