Multidimensional Response Surface Methodology for the development of a gene editing protocol for p67phox-deficient Chronic Granulomatous Disease.

IF 3.9 3区医学 Q2 BIOTECHNOLOGY & APPLIED MICROBIOLOGY Human gene therapy Pub Date : 2023-12-07 DOI:10.1089/hum.2023.114

Thomas E. Whittaker, Shefta-E Moula, Sameer Bahal, Faris G Bakri, W. Hayajneh, Ammar K Daoud, Asma Naseem, Alessia Cavazza, A. Thrasher, G. Santilli

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用多维响应面方法开发 p67phox 缺陷型慢性肉芽肿病的基因编辑方案。

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来源期刊

Human gene therapy 医学-生物工程与应用微生物

CiteScore

6.50

自引率

4.80%

发文量

131

审稿时长

4-8 weeks

期刊介绍： Human Gene Therapy is the premier, multidisciplinary journal covering all aspects of gene therapy. The Journal publishes in-depth coverage of DNA, RNA, and cell therapies by delivering the latest breakthroughs in research and technologies. Human Gene Therapy provides a central forum for scientific and clinical information, including ethical, legal, regulatory, social, and commercial issues, which enables the advancement and progress of therapeutic procedures leading to improved patient outcomes, and ultimately, to curing diseases.

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