Gene Editing based Targeted Integration for Correction of the Wiskott-Aldrich Syndrome

Melissa Pille, John M. Avila, So Hyun Park, Cuong Q. Le, Haipeng Xue, F. Haerynck, Lavanya Saxena, Ciaran M. Lee, E. Shpall, Gang Bao, Bart Vandekerckhove, Brian R. Davis
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