Therapeutic Role of Nusinersen on Respiratory Progression in Pediatric Patients With Spinal Muscular Atrophy Type 2 and Nonambulant Type 3

Federica Trucco, D. Ridout, H. Weststrate, M. Scoto, A. Rohwer, G. Coratti, Marion Main, Anna G. Mayhew, Jacqueline Montes, R. de Sanctis, Marika Pane, M. Pera, Valeria Sansone, E. Albamonte, Adele D'Amico, Claudio Bruno, Sonia Messina, A. Childs, Tracey Willis, Min Ong, Laurent Servais, Anirban Majumdar, Imelda Hughes, Chiara Marini-Bettolo, D. Parasuraman, V. Gowda, Giovanni Baranello, Enrico Bertini, D. D. De Vivo, Basil T. Darras, J. Day, Oscar Mayer, Z. Zolkipli-Cunningham, Richard S. Finkel, Eugenio Mercuri, Francesco Muntoni
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纽西奈森对脊髓性肌肉萎缩症 2 型和非游走性 3 型小儿患者呼吸系统进展的治疗作用
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