Pomalidomide for Epistaxis in Hereditary Hemorrhagic Telangiectasia

IF 96.2 1区医学 Q1 MEDICINE, GENERAL & INTERNAL New England Journal of Medicine Pub Date : 2024-09-19 DOI:10.1056/nejmoa2312749

Hanny Al-Samkari, Raj S. Kasthuri, Vivek N. Iyer, Allyson M. Pishko, Jake E. Decker, Clifford R. Weiss, Kevin J. Whitehead, Miles B. Conrad, Marc S. Zumberg, Jenny Y. Zhou, Joseph Parambil, Derek Marsh, Marianne Clancy, Lauren Bradley, Lisa Wisniewski, Benjamin A. Carper, Sonia M. Thomas, and Keith R. McCrae From Massachusetts General Hospital, Boston (H.A.-S.), University of North Carolina, Chapel Hill (R.S.K.), and RTI International, Research Triangle Park (D.M., L.B., B.A.C., S.M.T.) — both in North Carolina, Mayo Clinic, Rochester, MN (V.N.I.), University of Pennsylvania, Philadelphia (A.M.P.), Medical College of Wisconsin, Milwaukee (J.E.D.), Johns Hopkins University, Baltimore (C.R.W.), and CureHHT, Monkton (M.C.) — both in Maryland, University of Utah, Salt Lake City (K.J.W.), University of California, San Francisco, San Francisco (M.B.C.), University of Florida, Gainesville (M.S.Z.), University of California, San Diego, La Jolla (J.Y.Z.), and Taussig ..

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Abstract

Hereditary hemorrhagic telangiectasia (HHT) is characterized by extensive telangiectasias and arteriovenous malformations. The primary clinical manifestation is epistaxis that results in iron-defic...

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来源期刊

New England Journal of Medicine 医学-医学：内科

CiteScore

145.40

自引率

0.60%

发文量

1839

审稿时长

1 months

期刊介绍： The New England Journal of Medicine (NEJM) stands as the foremost medical journal and website worldwide. With an impressive history spanning over two centuries, NEJM boasts a consistent publication of superb, peer-reviewed research and engaging clinical content. Our primary objective revolves around delivering high-caliber information and findings at the juncture of biomedical science and clinical practice. We strive to present this knowledge in formats that are not only comprehensible but also hold practical value, effectively influencing healthcare practices and ultimately enhancing patient outcomes.

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