Living, not just surviving, with chronic myeloid leukemia – quality of life to the front of the line

IF 13.4 1区 医学 Q1 HEMATOLOGY Leukemia Pub Date : 2025-03-05 DOI:10.1038/s41375-025-02548-z
Jeffrey H. Lipton, Delphine Rea
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生活,而不仅仅是生存,与慢性髓性白血病-生活质量的前线
慢性髓性白血病(CML)的治疗在过去的三十年中取得了长足的进步。从一种有治疗选择的疾病到一小部分新诊断的患者,即使是这样,也有可能出现重大的治疗相关问题,如果诊断为慢性期,患者的生存率现在接近于一般人群中年龄匹配的对照组,患者的依从性很好,并且药物可用。是的,我们可以讨论几个百分点的改善是否值得使用非常新的和更昂贵的药物,这些药物在世界上大部分地区都无法获得,但我们现在有一种疾病,无病生存率高于总体生存率,这表明人们的死亡不是意外的,但通常不是死于慢性粒细胞白血病!CML管理方面的重大改进,无论是在可用药物方面,还是毫无疑问的,我们利用分子技术监测疾病反应或反应丧失的能力,现在都是常规可用的,并且使患者和治疗医生都更容易做到这一点。有人可能会认为,随着生存的改善,这将是给病人最满意的问题。最近以病人为导向的调查表明,这可能不是真的,我们作为医生认为最重要的,对病人来说往往是不一样的。
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来源期刊
Leukemia
Leukemia 医学-血液学
CiteScore
18.10
自引率
3.50%
发文量
270
审稿时长
3-6 weeks
期刊介绍: Title: Leukemia Journal Overview: Publishes high-quality, peer-reviewed research Covers all aspects of research and treatment of leukemia and allied diseases Includes studies of normal hemopoiesis due to comparative relevance Topics of Interest: Oncogenes Growth factors Stem cells Leukemia genomics Cell cycle Signal transduction Molecular targets for therapy And more Content Types: Original research articles Reviews Letters Correspondence Comments elaborating on significant advances and covering topical issues
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