Lu Qiao,Carrie L Welch,Rebecca Hernan,Julia Wynn,Usha S Krishnan,Jill M Zalieckas,Terry Buchmiller,Julie Khlevner,Aliva De,Christiana Farkouh-Karoleski,Amy J Wagner,Andreas Heydweiller,Andreas C Mueller,Annelies de Klein,Brad W Warner,Carlo Maj,Dai Chung,David J McCulley,David Schindel,Douglas Potoka,Elizabeth Fialkowski,Felicitas Schulz,Florian Kipfmuller,Foong-Yen Lim,Frank Magielsen,George B Mychaliska,Gudrun Aspelund,Heiko Martin Reutter,Howard Needelman,J Marco Schnater,Jason C Fisher,Kenneth Azarow,Mahmoud Elfiky,Markus M Nöthen,Melissa E Danko,Mindy Li,Przemyslaw Kosiński,Rene M H Wijnen,Robert A Cusick,Samuel Z Soffer,Suzan C M Cochius-Den Otter,Thomas Schaible,Timothy Crombleholme,Vincent P Duron,Patricia K Donahoe,Xin Sun,Frances A High,Charlotte Bendixen,Erwin Brosens,Yufeng Shen,Wendy K Chung
{"title":"在新变异的背景下,常见变异会增加先天性膈疝的风险。","authors":"Lu Qiao,Carrie L Welch,Rebecca Hernan,Julia Wynn,Usha S Krishnan,Jill M Zalieckas,Terry Buchmiller,Julie Khlevner,Aliva De,Christiana Farkouh-Karoleski,Amy J Wagner,Andreas Heydweiller,Andreas C Mueller,Annelies de Klein,Brad W Warner,Carlo Maj,Dai Chung,David J McCulley,David Schindel,Douglas Potoka,Elizabeth Fialkowski,Felicitas Schulz,Florian Kipfmuller,Foong-Yen Lim,Frank Magielsen,George B Mychaliska,Gudrun Aspelund,Heiko Martin Reutter,Howard Needelman,J Marco Schnater,Jason C Fisher,Kenneth Azarow,Mahmoud Elfiky,Markus M Nöthen,Melissa E Danko,Mindy Li,Przemyslaw Kosiński,Rene M H Wijnen,Robert A Cusick,Samuel Z Soffer,Suzan C M Cochius-Den Otter,Thomas Schaible,Timothy Crombleholme,Vincent P Duron,Patricia K Donahoe,Xin Sun,Frances A High,Charlotte Bendixen,Erwin Brosens,Yufeng Shen,Wendy K Chung","doi":"10.1016/j.ajhg.2024.08.024","DOIUrl":null,"url":null,"abstract":"Congenital diaphragmatic hernia (CDH) is a severe congenital anomaly often accompanied by other structural anomalies and/or neurobehavioral manifestations. Rare de novo protein-coding variants and copy-number variations contribute to CDH in the population. However, most individuals with CDH remain genetically undiagnosed. Here, we perform integrated de novo and common-variant analyses using 1,469 CDH individuals, including 1,064 child-parent trios and 6,133 ancestry-matched, unaffected controls for the genome-wide association study. We identify candidate CDH variants in 15 genes, including eight novel genes, through deleterious de novo variants. We further identify two genomic loci contributing to CDH risk through common variants with similar effect sizes among Europeans and Latinx. Both loci are in putative transcriptional regulatory regions of developmental patterning genes. Estimated heritability in common variants is ∼19%. Strikingly, there is no significant difference in estimated polygenic risk scores between isolated and complex CDH or between individuals harboring deleterious de novo variants and individuals without these variants. The data support a polygenic model as part of the CDH genetic architecture.","PeriodicalId":7659,"journal":{"name":"American journal of human genetics","volume":"37 1","pages":""},"PeriodicalIF":8.1000,"publicationDate":"2024-09-24","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":"0","resultStr":"{\"title\":\"Common variants increase risk for congenital diaphragmatic hernia within the context of de novo variants.\",\"authors\":\"Lu Qiao,Carrie L Welch,Rebecca Hernan,Julia Wynn,Usha S Krishnan,Jill M Zalieckas,Terry Buchmiller,Julie Khlevner,Aliva De,Christiana Farkouh-Karoleski,Amy J Wagner,Andreas Heydweiller,Andreas C Mueller,Annelies de Klein,Brad W Warner,Carlo Maj,Dai Chung,David J McCulley,David Schindel,Douglas Potoka,Elizabeth Fialkowski,Felicitas Schulz,Florian Kipfmuller,Foong-Yen Lim,Frank Magielsen,George B Mychaliska,Gudrun Aspelund,Heiko Martin Reutter,Howard Needelman,J Marco Schnater,Jason C Fisher,Kenneth Azarow,Mahmoud Elfiky,Markus M Nöthen,Melissa E Danko,Mindy Li,Przemyslaw Kosiński,Rene M H Wijnen,Robert A Cusick,Samuel Z Soffer,Suzan C M Cochius-Den Otter,Thomas Schaible,Timothy Crombleholme,Vincent P Duron,Patricia K Donahoe,Xin Sun,Frances A High,Charlotte Bendixen,Erwin Brosens,Yufeng Shen,Wendy K Chung\",\"doi\":\"10.1016/j.ajhg.2024.08.024\",\"DOIUrl\":null,\"url\":null,\"abstract\":\"Congenital diaphragmatic hernia (CDH) is a severe congenital anomaly often accompanied by other structural anomalies and/or neurobehavioral manifestations. Rare de novo protein-coding variants and copy-number variations contribute to CDH in the population. However, most individuals with CDH remain genetically undiagnosed. Here, we perform integrated de novo and common-variant analyses using 1,469 CDH individuals, including 1,064 child-parent trios and 6,133 ancestry-matched, unaffected controls for the genome-wide association study. We identify candidate CDH variants in 15 genes, including eight novel genes, through deleterious de novo variants. We further identify two genomic loci contributing to CDH risk through common variants with similar effect sizes among Europeans and Latinx. Both loci are in putative transcriptional regulatory regions of developmental patterning genes. Estimated heritability in common variants is ∼19%. Strikingly, there is no significant difference in estimated polygenic risk scores between isolated and complex CDH or between individuals harboring deleterious de novo variants and individuals without these variants. The data support a polygenic model as part of the CDH genetic architecture.\",\"PeriodicalId\":7659,\"journal\":{\"name\":\"American journal of human genetics\",\"volume\":\"37 1\",\"pages\":\"\"},\"PeriodicalIF\":8.1000,\"publicationDate\":\"2024-09-24\",\"publicationTypes\":\"Journal Article\",\"fieldsOfStudy\":null,\"isOpenAccess\":false,\"openAccessPdf\":\"\",\"citationCount\":\"0\",\"resultStr\":null,\"platform\":\"Semanticscholar\",\"paperid\":null,\"PeriodicalName\":\"American journal of human genetics\",\"FirstCategoryId\":\"99\",\"ListUrlMain\":\"https://doi.org/10.1016/j.ajhg.2024.08.024\",\"RegionNum\":1,\"RegionCategory\":\"生物学\",\"ArticlePicture\":[],\"TitleCN\":null,\"AbstractTextCN\":null,\"PMCID\":null,\"EPubDate\":\"\",\"PubModel\":\"\",\"JCR\":\"Q1\",\"JCRName\":\"GENETICS & HEREDITY\",\"Score\":null,\"Total\":0}","platform":"Semanticscholar","paperid":null,"PeriodicalName":"American journal of human genetics","FirstCategoryId":"99","ListUrlMain":"https://doi.org/10.1016/j.ajhg.2024.08.024","RegionNum":1,"RegionCategory":"生物学","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":null,"EPubDate":"","PubModel":"","JCR":"Q1","JCRName":"GENETICS & HEREDITY","Score":null,"Total":0}
Common variants increase risk for congenital diaphragmatic hernia within the context of de novo variants.
Congenital diaphragmatic hernia (CDH) is a severe congenital anomaly often accompanied by other structural anomalies and/or neurobehavioral manifestations. Rare de novo protein-coding variants and copy-number variations contribute to CDH in the population. However, most individuals with CDH remain genetically undiagnosed. Here, we perform integrated de novo and common-variant analyses using 1,469 CDH individuals, including 1,064 child-parent trios and 6,133 ancestry-matched, unaffected controls for the genome-wide association study. We identify candidate CDH variants in 15 genes, including eight novel genes, through deleterious de novo variants. We further identify two genomic loci contributing to CDH risk through common variants with similar effect sizes among Europeans and Latinx. Both loci are in putative transcriptional regulatory regions of developmental patterning genes. Estimated heritability in common variants is ∼19%. Strikingly, there is no significant difference in estimated polygenic risk scores between isolated and complex CDH or between individuals harboring deleterious de novo variants and individuals without these variants. The data support a polygenic model as part of the CDH genetic architecture.
期刊介绍:
The American Journal of Human Genetics (AJHG) is a monthly journal published by Cell Press, chosen by The American Society of Human Genetics (ASHG) as its premier publication starting from January 2008. AJHG represents Cell Press's first society-owned journal, and both ASHG and Cell Press anticipate significant synergies between AJHG content and that of other Cell Press titles.