Pub Date : 2025-12-01DOI: 10.1016/j.jval.2025.09.3056
Will King MPH , Valeria M. Toledo-Gallegos PhD , Sarah Hill PhD , Yemi Oluboyede MSc, PhD
{"title":"P37 Advancing Preference Elicitation Techniques for Rare Diseases and Limited Sample Populations","authors":"Will King MPH , Valeria M. Toledo-Gallegos PhD , Sarah Hill PhD , Yemi Oluboyede MSc, PhD","doi":"10.1016/j.jval.2025.09.3056","DOIUrl":"10.1016/j.jval.2025.09.3056","url":null,"abstract":"","PeriodicalId":23508,"journal":{"name":"Value in Health","volume":"28 12","pages":"Page S34"},"PeriodicalIF":6.0,"publicationDate":"2025-12-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"145766060","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":2,"RegionCategory":"医学","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
Pub Date : 2025-12-01DOI: 10.1016/j.jval.2025.09.092
Emma Benbow MA, PhD , Tim Reason BSc, MSc , Cheryl Jayne Jones BSc, MSc, PhD , Sven L. Klijn MSc , Bill Malcolm MSc
{"title":"P53 Exploring the Ability of Generative AI to Interpret and Report Comprehensive NMA Results: A Step Towards the Automation of NMA Reports","authors":"Emma Benbow MA, PhD , Tim Reason BSc, MSc , Cheryl Jayne Jones BSc, MSc, PhD , Sven L. Klijn MSc , Bill Malcolm MSc","doi":"10.1016/j.jval.2025.09.092","DOIUrl":"10.1016/j.jval.2025.09.092","url":null,"abstract":"","PeriodicalId":23508,"journal":{"name":"Value in Health","volume":"28 12","pages":"Pages S37-S38"},"PeriodicalIF":6.0,"publicationDate":"2025-12-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"145766095","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":2,"RegionCategory":"医学","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
Pub Date : 2025-12-01DOI: 10.1016/j.jval.2025.09.145
Khaled M. Musallam PhD, MD , Maria Domenica Cappellini MD , Janet L. Kwiatkowski MD, MSCE , Vanessa Shih MS, PharmD , Amey Rane BS, MS , Keely Gilroy PhD , Emma Chatterton BSc, MRes , Katie Lewis BSc , Brianne Kerr BSc , Ali T. Taher MD, PhD, FRCP
{"title":"CO43 Clinical Burden and Transfusion-Related Outcomes in Transfusion-Dependent Thalassemia in the Kingdom of Saudi Arabia and United Arab Emirates","authors":"Khaled M. Musallam PhD, MD , Maria Domenica Cappellini MD , Janet L. Kwiatkowski MD, MSCE , Vanessa Shih MS, PharmD , Amey Rane BS, MS , Keely Gilroy PhD , Emma Chatterton BSc, MRes , Katie Lewis BSc , Brianne Kerr BSc , Ali T. Taher MD, PhD, FRCP","doi":"10.1016/j.jval.2025.09.145","DOIUrl":"10.1016/j.jval.2025.09.145","url":null,"abstract":"","PeriodicalId":23508,"journal":{"name":"Value in Health","volume":"28 12","pages":"Page S49"},"PeriodicalIF":6.0,"publicationDate":"2025-12-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"145765672","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":2,"RegionCategory":"医学","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
Pub Date : 2025-12-01DOI: 10.1016/j.jval.2025.09.067
Cherrishe Brown-Bickerstaff MPH, PhD , Paul R. Conkling MD , Zhaohui Su PhD , Jessica Paulus ScD , Malcolm Charles MS , Daniel Schlauch PhD
{"title":"P24 A Framework for Accelerating Clinical Development With Real-World External Control Arms (ECA) in Phase 2 Trials","authors":"Cherrishe Brown-Bickerstaff MPH, PhD , Paul R. Conkling MD , Zhaohui Su PhD , Jessica Paulus ScD , Malcolm Charles MS , Daniel Schlauch PhD","doi":"10.1016/j.jval.2025.09.067","DOIUrl":"10.1016/j.jval.2025.09.067","url":null,"abstract":"","PeriodicalId":23508,"journal":{"name":"Value in Health","volume":"28 12","pages":"Page S31"},"PeriodicalIF":6.0,"publicationDate":"2025-12-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"145765894","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":2,"RegionCategory":"医学","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
Pub Date : 2025-12-01DOI: 10.1016/j.jval.2025.09.113
Maria Rosaria Villa MD , Abel Hassoun MD, PhD , Korinna Karampampa MSc, PhD , Ying Yang PhD , Marco Panebianco MSc , Mariano Ratto MSc , Xiang Zhang PhD , Florian Langer MD
{"title":"CO10 Analysis of Pooled Real-World Utilization and Outcomes Data of rVIII-Single Chain Compared With Standard and Extended Half-Life FVIII Products for Prophylaxis of Hemophilia A in France, Germany, and Italy","authors":"Maria Rosaria Villa MD , Abel Hassoun MD, PhD , Korinna Karampampa MSc, PhD , Ying Yang PhD , Marco Panebianco MSc , Mariano Ratto MSc , Xiang Zhang PhD , Florian Langer MD","doi":"10.1016/j.jval.2025.09.113","DOIUrl":"10.1016/j.jval.2025.09.113","url":null,"abstract":"","PeriodicalId":23508,"journal":{"name":"Value in Health","volume":"28 12","pages":"Page S43"},"PeriodicalIF":6.0,"publicationDate":"2025-12-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"145765965","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":2,"RegionCategory":"医学","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
Pub Date : 2025-12-01DOI: 10.1016/j.jval.2025.09.136
Paul E. Kearney PhD , Abdool F. Bhollah MSc , Eric Stanek PhD
{"title":"CO34 Budget Impact of a PreTRM-Guided Preventive Bundle for Preterm Birth in Low-Risk Pregnancies: A Microsimulation Study Using PRIME Trial Data","authors":"Paul E. Kearney PhD , Abdool F. Bhollah MSc , Eric Stanek PhD","doi":"10.1016/j.jval.2025.09.136","DOIUrl":"10.1016/j.jval.2025.09.136","url":null,"abstract":"","PeriodicalId":23508,"journal":{"name":"Value in Health","volume":"28 12","pages":"Pages S47-S48"},"PeriodicalIF":6.0,"publicationDate":"2025-12-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"145766035","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":2,"RegionCategory":"医学","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
Pub Date : 2025-12-01DOI: 10.1016/j.jval.2025.09.142
José Silva-Nunes M.D, PhD , António Teixeira-Rodrigues phD , JOSÉ GUERREIRO BSc , Carolina Rojais MSc , Vasco Miguel Gomes Conde PharmD , Maria Cary MSc , Joao Sergio Neves M.D, PhD
{"title":"CO40 Characterization of the Distribution of Body Mass Index in Portuguese People With Type 2 Diabetes","authors":"José Silva-Nunes M.D, PhD , António Teixeira-Rodrigues phD , JOSÉ GUERREIRO BSc , Carolina Rojais MSc , Vasco Miguel Gomes Conde PharmD , Maria Cary MSc , Joao Sergio Neves M.D, PhD","doi":"10.1016/j.jval.2025.09.142","DOIUrl":"10.1016/j.jval.2025.09.142","url":null,"abstract":"","PeriodicalId":23508,"journal":{"name":"Value in Health","volume":"28 12","pages":"Page S48"},"PeriodicalIF":6.0,"publicationDate":"2025-12-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"145766101","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":2,"RegionCategory":"医学","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}