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SILENT CONVERSATIONS: JMML'S INTERPLAY WITH T CELL 沉默的对话:jml与t细胞的相互作用
Pub Date : 2025-11-04 DOI: 10.1016/j.ejcped.2025.100415
Jovana Rajak , Ke Meng , Anna Lena Sippel , Jun Wang , Naile Koleci , Alexandra Emilia Schlaak , Hui Xiao , Riccardo Masseti , Christian Flotho , Charlotte M. Niemeyer , Luciana Hannibal , Bertram Bengsch , Miriam Erlacher
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引用次数: 0
ALTERNATIVE DONOR PERIPHERAL STEM CELL TRANSPLANTATION WITH TCRΑΒ/CD19 DEPLETION FOR PEDIATRIC PATIENTS WITH BONE MARROW FAILURE 替代供体外周干细胞移植与tcrΑΒ / cd19缺失治疗小儿骨髓衰竭
Pub Date : 2025-11-04 DOI: 10.1016/j.ejcped.2025.100324
Caitlin W. Elgarten , Joseph H. Oved , Lisa Wray , Kimberly Venella , Peter Nicholas , Stephan Kadauke , Yongping Wang , Stephan Grupp , Timothy S. Olson
{"title":"ALTERNATIVE DONOR PERIPHERAL STEM CELL TRANSPLANTATION WITH TCRΑΒ/CD19 DEPLETION FOR PEDIATRIC PATIENTS WITH BONE MARROW FAILURE","authors":"Caitlin W. Elgarten , Joseph H. Oved , Lisa Wray , Kimberly Venella , Peter Nicholas , Stephan Kadauke , Yongping Wang , Stephan Grupp , Timothy S. Olson","doi":"10.1016/j.ejcped.2025.100324","DOIUrl":"10.1016/j.ejcped.2025.100324","url":null,"abstract":"","PeriodicalId":94314,"journal":{"name":"EJC paediatric oncology","volume":"6 ","pages":"Article 100324"},"PeriodicalIF":0.0,"publicationDate":"2025-11-04","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"145428305","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
引用次数: 0
A SINGLE-CENTER RETROSPECTIVE ANALYSIS OF TRANSPLANTATION OUTCOMES IN PATIENTS WITH JUVENILE MYELOMONOCYTIC LEUKEMIA 少年髓单细胞白血病患者移植结果的单中心回顾性分析
Pub Date : 2025-11-04 DOI: 10.1016/j.ejcped.2025.100388
Li Xiaolan, Wan Yang, Liu Lipeng, Zhang Aoli, Zhang Xiaoyan, Chen Xia, Ren Yuanyuan, Liu Xiaoming, Guo Ye, Yang Wenyu, Liu Fang
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引用次数: 0
IN VITRO MODEL OF STAGE-SPECIFIC EVOLUTION OF CLONAL HEMATOPOIESIS IN CN TO CN/AML 克隆造血在中国到中国的阶段特异性进化的体外模型
Pub Date : 2025-11-04 DOI: 10.1016/j.ejcped.2025.100340
Natalia Borbaran Bravo, Anna-Sophia Hellmuth, Sergey Kandabarau, Maksim Klimiankou, Julia Skokowa
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引用次数: 0
MYELOPROLIFERATIVE NEOPLASMS (MPN) DIAGNOSED IN CHILDHOOD AND ADOLESCENCE – PROSPECTIVE DATA ON CLINICAL AND GENETIC CHARACTERISTICS FROM THE GERMAN NATIONAL MPN CHILDHOOD REGISTRY 儿童期和青春期诊断的骨髓增生性肿瘤(mpn) -来自德国国家mpn儿童登记处的临床和遗传特征的前瞻性数据
Pub Date : 2025-11-04 DOI: 10.1016/j.ejcped.2025.100347
Yvonne Lisa Behrens , Thea Reinkens , Winfried Hofmann , Amelie Gumann , Renate Strasser , Paulin Wanjek , Nataliya Di Donato , Lara Seitz , Martina Pontones , Franziska Fahrmeier , Marc-Phillip Hitz , Zofia Wotschofsky , Brigitte Schlegelberger , Tim Ripperger , Axel Karow
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引用次数: 0
GENETIC LANDSCAPE OF MYELODYSPLASTIC SYNDROME IN CHILDREN 儿童骨髓增生异常综合征的遗传景观
Pub Date : 2025-11-04 DOI: 10.1016/j.ejcped.2025.100349
Masataka Hasegawa , Kaito Mimura , Rintaro Ono , Dai Keino , Shinichi Tsujimoto , Kiyotaka Isobe , Takao Deguchi , Hideto Iwafuchi , Hiroshi Moritake , Atsushi Manabe , Seishi Ogawa , Kenichi Yoshida , Daisuke Hasegawa
{"title":"GENETIC LANDSCAPE OF MYELODYSPLASTIC SYNDROME IN CHILDREN","authors":"Masataka Hasegawa , Kaito Mimura , Rintaro Ono , Dai Keino , Shinichi Tsujimoto , Kiyotaka Isobe , Takao Deguchi , Hideto Iwafuchi , Hiroshi Moritake , Atsushi Manabe , Seishi Ogawa , Kenichi Yoshida , Daisuke Hasegawa","doi":"10.1016/j.ejcped.2025.100349","DOIUrl":"10.1016/j.ejcped.2025.100349","url":null,"abstract":"","PeriodicalId":94314,"journal":{"name":"EJC paediatric oncology","volume":"6 ","pages":"Article 100349"},"PeriodicalIF":0.0,"publicationDate":"2025-11-04","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"145428522","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
引用次数: 0
FAVORABLE LONG-TERM OUTCOMES WITH IMMUNOSUPPRESSIVE THERAPY IN CHILDREN WITH SEVERE APLASTIC ANEMIA 免疫抑制治疗对重度再生障碍性贫血儿童的长期疗效有利
Pub Date : 2025-11-04 DOI: 10.1016/j.ejcped.2025.100359
Charikleia Kelaidi , Loizos Petrikkos , Kalliopi Stefanaki , Kalliopi Manola , Marianna Tzanoudaki , Vassilios Papadakis , Sophia Polychronopoulou
{"title":"FAVORABLE LONG-TERM OUTCOMES WITH IMMUNOSUPPRESSIVE THERAPY IN CHILDREN WITH SEVERE APLASTIC ANEMIA","authors":"Charikleia Kelaidi , Loizos Petrikkos , Kalliopi Stefanaki , Kalliopi Manola , Marianna Tzanoudaki , Vassilios Papadakis , Sophia Polychronopoulou","doi":"10.1016/j.ejcped.2025.100359","DOIUrl":"10.1016/j.ejcped.2025.100359","url":null,"abstract":"","PeriodicalId":94314,"journal":{"name":"EJC paediatric oncology","volume":"6 ","pages":"Article 100359"},"PeriodicalIF":0.0,"publicationDate":"2025-11-04","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"145428532","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
引用次数: 0
CLINICAL AND LABORATORY CHARACTERISTICS OF IST (IMMUNE SUPPRESSION THERAPY) RESPONDERS (ISTR) AND NON-RESPONDERS (ISTN) IN SWISS PEDIATRIC PATIENTS WITH SAA OR HYPOCELLULAR RCC 瑞士儿童saa或低细胞RCC患者免疫抑制治疗应答者(istr)和无应答者(istn)的临床和实验室特征
Pub Date : 2025-11-04 DOI: 10.1016/j.ejcped.2025.100360
E Picotti , C. Gengler , T Güngör , M. Amrein , R. Renella , U. Tanriver , A. Klein-Franke , A. Yoshimi , M. Schmugge
{"title":"CLINICAL AND LABORATORY CHARACTERISTICS OF IST (IMMUNE SUPPRESSION THERAPY) RESPONDERS (ISTR) AND NON-RESPONDERS (ISTN) IN SWISS PEDIATRIC PATIENTS WITH SAA OR HYPOCELLULAR RCC","authors":"E Picotti , C. Gengler , T Güngör , M. Amrein , R. Renella , U. Tanriver , A. Klein-Franke , A. Yoshimi , M. Schmugge","doi":"10.1016/j.ejcped.2025.100360","DOIUrl":"10.1016/j.ejcped.2025.100360","url":null,"abstract":"","PeriodicalId":94314,"journal":{"name":"EJC paediatric oncology","volume":"6 ","pages":"Article 100360"},"PeriodicalIF":0.0,"publicationDate":"2025-11-04","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"145428533","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
引用次数: 0
EPIGENETIC MECHANISMS AND THERAPEUTIC VULNERABILITIES IN A GATA2 HAPLOINSUFFICIENT MOUSE MODEL gata2单倍不足小鼠模型的表观遗传机制和治疗脆弱性
Pub Date : 2025-11-04 DOI: 10.1016/j.ejcped.2025.100368
Juncal Fernandez-Orth , Marina AlcaidMiranda , Julia M. Weiss , Alessandra Sandrina , Eric TorralbaSales , Esteban Ballestar , Geoffroy Andrieux , Melanie Borries , Miriam Erlacher
{"title":"EPIGENETIC MECHANISMS AND THERAPEUTIC VULNERABILITIES IN A GATA2 HAPLOINSUFFICIENT MOUSE MODEL","authors":"Juncal Fernandez-Orth , Marina AlcaidMiranda , Julia M. Weiss , Alessandra Sandrina , Eric TorralbaSales , Esteban Ballestar , Geoffroy Andrieux , Melanie Borries , Miriam Erlacher","doi":"10.1016/j.ejcped.2025.100368","DOIUrl":"10.1016/j.ejcped.2025.100368","url":null,"abstract":"","PeriodicalId":94314,"journal":{"name":"EJC paediatric oncology","volume":"6 ","pages":"Article 100368"},"PeriodicalIF":0.0,"publicationDate":"2025-11-04","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"145428554","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
引用次数: 0
INTEGRATION OF A BONE MARROW FAILURE GERMLINE PANEL INTO THE COMPREHENSIVE CLINICAL GENOMICS PIPELINE AT ST. JUDE CHILDREN’S RESEARCH HOSPITAL: INSIGHTS FROM 22 MONTHS’ EXPERIENCE st. Jude儿童研究型医院将骨髓衰竭生殖细胞小组整合到综合临床基因组学管道中:来自22个月经验的见解
Pub Date : 2025-11-04 DOI: 10.1016/j.ejcped.2025.100375
Victor Pastor Loyola , Enrico Attardi , Jamie Maciaszek , Sara Lewis , Taylor Cain , Passant Shaker , Nathan Gray , Michelle Boals , Jennifer Neary , Mark Wilkinson , Michael Rusch , Lu Wang , Jeffery Klco , Marcin Wlodarski
{"title":"INTEGRATION OF A BONE MARROW FAILURE GERMLINE PANEL INTO THE COMPREHENSIVE CLINICAL GENOMICS PIPELINE AT ST. JUDE CHILDREN’S RESEARCH HOSPITAL: INSIGHTS FROM 22 MONTHS’ EXPERIENCE","authors":"Victor Pastor Loyola , Enrico Attardi , Jamie Maciaszek , Sara Lewis , Taylor Cain , Passant Shaker , Nathan Gray , Michelle Boals , Jennifer Neary , Mark Wilkinson , Michael Rusch , Lu Wang , Jeffery Klco , Marcin Wlodarski","doi":"10.1016/j.ejcped.2025.100375","DOIUrl":"10.1016/j.ejcped.2025.100375","url":null,"abstract":"","PeriodicalId":94314,"journal":{"name":"EJC paediatric oncology","volume":"6 ","pages":"Article 100375"},"PeriodicalIF":0.0,"publicationDate":"2025-11-04","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"145428561","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
引用次数: 0
期刊
EJC paediatric oncology
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