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IMPROVED OUTCOMES FOR PEDIATRIC PATIENTS WITH DE NOVO CHRONIC MYELOID LEUKEMIA IN BLAST PHASE BY EARLY STAGE ALLOGENEIC HEMATOPOIETIC STEM CELL TRANSPLANTATION 早期同种异体造血干细胞移植改善原发性慢性髓性白血病患儿的预后
Pub Date : 2025-11-04 DOI: 10.1016/j.ejcped.2025.100389
Li Xiaolan, Liu Lipeng, Zhang Aoli, Chen Xia, Ren Yuanyuan, Guo Ye, Zhu Xiaofan, Yang Wenyu, Liu Fang
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引用次数: 0
MALIGNANCY IN FANCONI APLASTIC ANEMIA; SINGLE CENTER EXPERIENCE 范可尼再障的恶性肿瘤;单中心体验
Pub Date : 2025-11-04 DOI: 10.1016/j.ejcped.2025.100396
Nihal Karadas , Ceylin Sengil , Ayse Gadashova , Cihan Onder , Burak Durmaz , Emin Karaca , Deniz Yilmaz Karapinar
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引用次数: 0
CELLULAR IMMUNOTHERAPY TARGETING CLL-1 FOR JUVENILE MYELOMONOCYTIC LEUKEMIA 针对细胞-1的细胞免疫疗法治疗青少年髓单细胞白血病
Pub Date : 2025-11-04 DOI: 10.1016/j.ejcped.2025.100418
Juwita Werner , Alex G. Lee , Sydney Abelson , Sherin Xirenayi , Khadija Yousuf , Hanna Shin , Bonell Patiño-Escobar , Abhilash Barpanda , Julia Meyer , Sarah K. Tasian , Arun P. Wiita , Elliot Stieglitz
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引用次数: 0
ASSESSMENT OF GENETIC TESTING FOLLOWING CURRENT COMPREHENSIVE CLINICAL DIAGNOSTIC EVALUATION FOR PEDIATRIC SEVERE APLASTIC ANEMIA 当前儿科严重再生障碍性贫血综合临床诊断评估后的基因检测评估
Pub Date : 2025-11-04 DOI: 10.1016/j.ejcped.2025.100328
Helen D. Reed , Jill L. O. de Jong , Melissa Gaviria , Ashwin Koppayi , Youssef Ahmed , Ian Atkinson , Margret Joos , Maggie Malsch , Matthew McClung , Peter Nicholas , Mancy Shah , Erin E. Sullivan , Hongbo Xie , Silvia Zavarella , Yu Zhou , Barry Zorman , Lucy A. Godley , Taizo A. Nakano , Timothy S. Olson , Alison A. Bertuch , Akiko Shimamura
{"title":"ASSESSMENT OF GENETIC TESTING FOLLOWING CURRENT COMPREHENSIVE CLINICAL DIAGNOSTIC EVALUATION FOR PEDIATRIC SEVERE APLASTIC ANEMIA","authors":"Helen D. Reed , Jill L. O. de Jong , Melissa Gaviria , Ashwin Koppayi , Youssef Ahmed , Ian Atkinson , Margret Joos , Maggie Malsch , Matthew McClung , Peter Nicholas , Mancy Shah , Erin E. Sullivan , Hongbo Xie , Silvia Zavarella , Yu Zhou , Barry Zorman , Lucy A. Godley , Taizo A. Nakano , Timothy S. Olson , Alison A. Bertuch , Akiko Shimamura","doi":"10.1016/j.ejcped.2025.100328","DOIUrl":"10.1016/j.ejcped.2025.100328","url":null,"abstract":"","PeriodicalId":94314,"journal":{"name":"EJC paediatric oncology","volume":"6 ","pages":"Article 100328"},"PeriodicalIF":0.0,"publicationDate":"2025-11-04","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"145428504","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
引用次数: 0
IN-VIVO MOUSE MODEL OF ACUTE MYELOID LEUKEMIA DEVELOPMENT IN CONGENITAL NEUTROPENIA 先天性中性粒细胞减少症急性髓性白血病发展的小鼠体内模型
Pub Date : 2025-11-04 DOI: 10.1016/j.ejcped.2025.100333
Jérémy Haaf, Malte Ritter, Patricia Arreba-Tutusaus, Siarhei Kandabarau, Maksim Klimiankou, Julia Skokowa
{"title":"IN-VIVO MOUSE MODEL OF ACUTE MYELOID LEUKEMIA DEVELOPMENT IN CONGENITAL NEUTROPENIA","authors":"Jérémy Haaf, Malte Ritter, Patricia Arreba-Tutusaus, Siarhei Kandabarau, Maksim Klimiankou, Julia Skokowa","doi":"10.1016/j.ejcped.2025.100333","DOIUrl":"10.1016/j.ejcped.2025.100333","url":null,"abstract":"","PeriodicalId":94314,"journal":{"name":"EJC paediatric oncology","volume":"6 ","pages":"Article 100333"},"PeriodicalIF":0.0,"publicationDate":"2025-11-04","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"145428509","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
引用次数: 0
MITOTIC DEFECTS IMPAIRED CD34+ PROLIFERATION IN GATA2 DEFICIENCY 有丝分裂缺陷损害了gata2缺乏时cd34 +的增殖
Pub Date : 2025-11-04 DOI: 10.1016/j.ejcped.2025.100335
Maria Magallon-Mosella , Damia Romero-Moya , Cristina Calvo , Joan Pera , Eric Torralba-Sales , Miriam Erlacher , Òscar Molina , Alessandra Giorgetti
{"title":"MITOTIC DEFECTS IMPAIRED CD34+ PROLIFERATION IN GATA2 DEFICIENCY","authors":"Maria Magallon-Mosella , Damia Romero-Moya , Cristina Calvo , Joan Pera , Eric Torralba-Sales , Miriam Erlacher , Òscar Molina , Alessandra Giorgetti","doi":"10.1016/j.ejcped.2025.100335","DOIUrl":"10.1016/j.ejcped.2025.100335","url":null,"abstract":"","PeriodicalId":94314,"journal":{"name":"EJC paediatric oncology","volume":"6 ","pages":"Article 100335"},"PeriodicalIF":0.0,"publicationDate":"2025-11-04","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"145428525","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
引用次数: 0
BH3-MIMETIC TREATMENT REVEALS SUBTYPE-SPECIFIC BCL-2 PROTEIN DEPENDENCY IN PEDIATRIC MDS WITH EXCESS BLASTS 模拟bh3治疗揭示了小儿MDS细胞过多的亚型特异性bcl-2蛋白依赖性
Pub Date : 2025-11-04 DOI: 10.1016/j.ejcped.2025.100355
Sheila Bohler , Ayami Yoshimi Nöllke , Nastassja Scheidegger , Ben Haladik , Beat Bornhauser , Michael N. Dworzak , Kaan Boztug , Markus Schmugge , Charlotte M. Niemeyer , Miriam Erlacher
{"title":"BH3-MIMETIC TREATMENT REVEALS SUBTYPE-SPECIFIC BCL-2 PROTEIN DEPENDENCY IN PEDIATRIC MDS WITH EXCESS BLASTS","authors":"Sheila Bohler , Ayami Yoshimi Nöllke , Nastassja Scheidegger , Ben Haladik , Beat Bornhauser , Michael N. Dworzak , Kaan Boztug , Markus Schmugge , Charlotte M. Niemeyer , Miriam Erlacher","doi":"10.1016/j.ejcped.2025.100355","DOIUrl":"10.1016/j.ejcped.2025.100355","url":null,"abstract":"","PeriodicalId":94314,"journal":{"name":"EJC paediatric oncology","volume":"6 ","pages":"Article 100355"},"PeriodicalIF":0.0,"publicationDate":"2025-11-04","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"145428528","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
引用次数: 0
STRATUS PRIMETM A GMP COMPLIANT PROCESS TO CREATE HIGH NUMBERS OF HLA COMPATIBLE DEFINITIVE HSPCS FROM IPSCS USING PIEZO1 AGONISTS Stratus primetm是一个符合GMP的流程,使用piezo1激动剂从ipscs中创建大量hla兼容的最终HSPCS
Pub Date : 2025-11-04 DOI: 10.1016/j.ejcped.2025.100356
Michael P. Cooke , Aayudh Das , Gurinder Singh , Zhi-Jian Liu , Qiao Lin , Sita Karan Patel , Jack Li , Vijaya G. Tirunagaru
{"title":"STRATUS PRIMETM A GMP COMPLIANT PROCESS TO CREATE HIGH NUMBERS OF HLA COMPATIBLE DEFINITIVE HSPCS FROM IPSCS USING PIEZO1 AGONISTS","authors":"Michael P. Cooke , Aayudh Das , Gurinder Singh , Zhi-Jian Liu , Qiao Lin , Sita Karan Patel , Jack Li , Vijaya G. Tirunagaru","doi":"10.1016/j.ejcped.2025.100356","DOIUrl":"10.1016/j.ejcped.2025.100356","url":null,"abstract":"","PeriodicalId":94314,"journal":{"name":"EJC paediatric oncology","volume":"6 ","pages":"Article 100356"},"PeriodicalIF":0.0,"publicationDate":"2025-11-04","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"145428529","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
引用次数: 0
ROMILOSTIM FOR TRTEATMENT OF CHILDREN AND YOUNG ADULTS WITH SEVERE APLASTIC ANEMIA AND MYELODYPLASTIC SYNDROME: A SINGLE CENTRE PILOT STUDY 罗米洛斯汀治疗患有严重再生障碍性贫血和骨髓发育不良综合征的儿童和年轻人:一项单中心试点研究
Pub Date : 2025-11-04 DOI: 10.1016/j.ejcped.2025.100365
Anjali Sharathkumar , David Claassen , Sarah Bell
{"title":"ROMILOSTIM FOR TRTEATMENT OF CHILDREN AND YOUNG ADULTS WITH SEVERE APLASTIC ANEMIA AND MYELODYPLASTIC SYNDROME: A SINGLE CENTRE PILOT STUDY","authors":"Anjali Sharathkumar , David Claassen , Sarah Bell","doi":"10.1016/j.ejcped.2025.100365","DOIUrl":"10.1016/j.ejcped.2025.100365","url":null,"abstract":"","PeriodicalId":94314,"journal":{"name":"EJC paediatric oncology","volume":"6 ","pages":"Article 100365"},"PeriodicalIF":0.0,"publicationDate":"2025-11-04","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"145428551","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
引用次数: 0
A FAMILY WITH MYSM1 MUTATION 一个mysm1突变的家庭
Pub Date : 2025-11-04 DOI: 10.1016/j.ejcped.2025.100367
Deniz Karapinar , Nihal Karadas , Ayami Yoshimi , Charlotte Niemeyer , Miriam Erlacher , Deniz Yilmaz Karapinar
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引用次数: 0
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EJC paediatric oncology
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