Pub Date : 2025-11-04DOI: 10.1016/j.ejcped.2025.100385
Rafael Balceiro , Neysimelia Costa Villela , Silva Eduardo Caetano Albino da , Glaucia Regina Costa Murra , Juliana Costa Gaspar , Silva Samia Frahia Bento da , Aline Tansini , Thais Regina Toledo de Santis , Luiz Fernando Lopes , Anita Frisanco Oliveira
{"title":"AZACITIDINE FOR PEDIATRIC PATIENTS WITH ADVANCED MYELODYSPLASTIC SYNDROME: EXPERIENCE FROM BRAZILIAN COOPERATIVE GROUP OF PEDIATRIC MYELODYSPLASTIC SYNDROME (GCB-SMD-PED)","authors":"Rafael Balceiro , Neysimelia Costa Villela , Silva Eduardo Caetano Albino da , Glaucia Regina Costa Murra , Juliana Costa Gaspar , Silva Samia Frahia Bento da , Aline Tansini , Thais Regina Toledo de Santis , Luiz Fernando Lopes , Anita Frisanco Oliveira","doi":"10.1016/j.ejcped.2025.100385","DOIUrl":"10.1016/j.ejcped.2025.100385","url":null,"abstract":"","PeriodicalId":94314,"journal":{"name":"EJC paediatric oncology","volume":"6 ","pages":"Article 100385"},"PeriodicalIF":0.0,"publicationDate":"2025-11-04","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"145428571","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
Pub Date : 2025-11-04DOI: 10.1016/j.ejcped.2025.100418
Juwita Werner , Alex G. Lee , Sydney Abelson , Sherin Xirenayi , Khadija Yousuf , Hanna Shin , Bonell Patiño-Escobar , Abhilash Barpanda , Julia Meyer , Sarah K. Tasian , Arun P. Wiita , Elliot Stieglitz
{"title":"CELLULAR IMMUNOTHERAPY TARGETING CLL-1 FOR JUVENILE MYELOMONOCYTIC LEUKEMIA","authors":"Juwita Werner , Alex G. Lee , Sydney Abelson , Sherin Xirenayi , Khadija Yousuf , Hanna Shin , Bonell Patiño-Escobar , Abhilash Barpanda , Julia Meyer , Sarah K. Tasian , Arun P. Wiita , Elliot Stieglitz","doi":"10.1016/j.ejcped.2025.100418","DOIUrl":"10.1016/j.ejcped.2025.100418","url":null,"abstract":"","PeriodicalId":94314,"journal":{"name":"EJC paediatric oncology","volume":"6 ","pages":"Article 100418"},"PeriodicalIF":0.0,"publicationDate":"2025-11-04","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"145428636","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
Pub Date : 2025-11-04DOI: 10.1016/j.ejcped.2025.100328
Helen D. Reed , Jill L. O. de Jong , Melissa Gaviria , Ashwin Koppayi , Youssef Ahmed , Ian Atkinson , Margret Joos , Maggie Malsch , Matthew McClung , Peter Nicholas , Mancy Shah , Erin E. Sullivan , Hongbo Xie , Silvia Zavarella , Yu Zhou , Barry Zorman , Lucy A. Godley , Taizo A. Nakano , Timothy S. Olson , Alison A. Bertuch , Akiko Shimamura
{"title":"ASSESSMENT OF GENETIC TESTING FOLLOWING CURRENT COMPREHENSIVE CLINICAL DIAGNOSTIC EVALUATION FOR PEDIATRIC SEVERE APLASTIC ANEMIA","authors":"Helen D. Reed , Jill L. O. de Jong , Melissa Gaviria , Ashwin Koppayi , Youssef Ahmed , Ian Atkinson , Margret Joos , Maggie Malsch , Matthew McClung , Peter Nicholas , Mancy Shah , Erin E. Sullivan , Hongbo Xie , Silvia Zavarella , Yu Zhou , Barry Zorman , Lucy A. Godley , Taizo A. Nakano , Timothy S. Olson , Alison A. Bertuch , Akiko Shimamura","doi":"10.1016/j.ejcped.2025.100328","DOIUrl":"10.1016/j.ejcped.2025.100328","url":null,"abstract":"","PeriodicalId":94314,"journal":{"name":"EJC paediatric oncology","volume":"6 ","pages":"Article 100328"},"PeriodicalIF":0.0,"publicationDate":"2025-11-04","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"145428504","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
Pub Date : 2025-11-04DOI: 10.1016/j.ejcped.2025.100356
Michael P. Cooke , Aayudh Das , Gurinder Singh , Zhi-Jian Liu , Qiao Lin , Sita Karan Patel , Jack Li , Vijaya G. Tirunagaru
{"title":"STRATUS PRIMETM A GMP COMPLIANT PROCESS TO CREATE HIGH NUMBERS OF HLA COMPATIBLE DEFINITIVE HSPCS FROM IPSCS USING PIEZO1 AGONISTS","authors":"Michael P. Cooke , Aayudh Das , Gurinder Singh , Zhi-Jian Liu , Qiao Lin , Sita Karan Patel , Jack Li , Vijaya G. Tirunagaru","doi":"10.1016/j.ejcped.2025.100356","DOIUrl":"10.1016/j.ejcped.2025.100356","url":null,"abstract":"","PeriodicalId":94314,"journal":{"name":"EJC paediatric oncology","volume":"6 ","pages":"Article 100356"},"PeriodicalIF":0.0,"publicationDate":"2025-11-04","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"145428529","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}