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EJC paediatric oncology最新文献

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AZACITIDINE FOR PEDIATRIC PATIENTS WITH ADVANCED MYELODYSPLASTIC SYNDROME: EXPERIENCE FROM BRAZILIAN COOPERATIVE GROUP OF PEDIATRIC MYELODYSPLASTIC SYNDROME (GCB-SMD-PED) 阿扎胞苷治疗小儿晚期骨髓增生异常综合征:巴西小儿骨髓增生异常综合征合作组(gcb-smd-ped)经验
Pub Date : 2025-11-04 DOI: 10.1016/j.ejcped.2025.100385
Rafael Balceiro , Neysimelia Costa Villela , Silva Eduardo Caetano Albino da , Glaucia Regina Costa Murra , Juliana Costa Gaspar , Silva Samia Frahia Bento da , Aline Tansini , Thais Regina Toledo de Santis , Luiz Fernando Lopes , Anita Frisanco Oliveira
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引用次数: 0
WHEN STANDARD TESTS FALL SHORT: SOLVING A COMPLEX CASE OF INHERITED BONE MARROW FAILURE SYNDROME THROUGH WHOLE-EXOME SEQUENCING 当标准测试不足时:通过全外显子组测序解决遗传性骨髓衰竭综合征的复杂病例
Pub Date : 2025-11-04 DOI: 10.1016/j.ejcped.2025.100370
Nicole Lelli , Carmelo Gurnari , Enrica Marchionni , Giorgia SIlvestrin , Giorgia Ranucci , Eugenia Ricci , Valentina Ferradin , Chiara Minotti , Susanna Gastaldi , Camilla Page , Cosimo DiRaimondo , Giuseppe Novelli , Federica Sangiuolo , Enrico Attardi , Maria Teresa Voso
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引用次数: 0
IMPROVED OUTCOMES FOR PEDIATRIC PATIENTS WITH DE NOVO CHRONIC MYELOID LEUKEMIA IN BLAST PHASE BY EARLY STAGE ALLOGENEIC HEMATOPOIETIC STEM CELL TRANSPLANTATION 早期同种异体造血干细胞移植改善原发性慢性髓性白血病患儿的预后
Pub Date : 2025-11-04 DOI: 10.1016/j.ejcped.2025.100389
Li Xiaolan, Liu Lipeng, Zhang Aoli, Chen Xia, Ren Yuanyuan, Guo Ye, Zhu Xiaofan, Yang Wenyu, Liu Fang
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引用次数: 0
MALIGNANCY IN FANCONI APLASTIC ANEMIA; SINGLE CENTER EXPERIENCE 范可尼再障的恶性肿瘤;单中心体验
Pub Date : 2025-11-04 DOI: 10.1016/j.ejcped.2025.100396
Nihal Karadas , Ceylin Sengil , Ayse Gadashova , Cihan Onder , Burak Durmaz , Emin Karaca , Deniz Yilmaz Karapinar
{"title":"MALIGNANCY IN FANCONI APLASTIC ANEMIA; SINGLE CENTER EXPERIENCE","authors":"Nihal Karadas , Ceylin Sengil , Ayse Gadashova , Cihan Onder , Burak Durmaz , Emin Karaca , Deniz Yilmaz Karapinar","doi":"10.1016/j.ejcped.2025.100396","DOIUrl":"10.1016/j.ejcped.2025.100396","url":null,"abstract":"","PeriodicalId":94314,"journal":{"name":"EJC paediatric oncology","volume":"6 ","pages":"Article 100396"},"PeriodicalIF":0.0,"publicationDate":"2025-11-04","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"145428613","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
引用次数: 0
CELLULAR IMMUNOTHERAPY TARGETING CLL-1 FOR JUVENILE MYELOMONOCYTIC LEUKEMIA 针对细胞-1的细胞免疫疗法治疗青少年髓单细胞白血病
Pub Date : 2025-11-04 DOI: 10.1016/j.ejcped.2025.100418
Juwita Werner , Alex G. Lee , Sydney Abelson , Sherin Xirenayi , Khadija Yousuf , Hanna Shin , Bonell Patiño-Escobar , Abhilash Barpanda , Julia Meyer , Sarah K. Tasian , Arun P. Wiita , Elliot Stieglitz
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引用次数: 0
ASSESSMENT OF GENETIC TESTING FOLLOWING CURRENT COMPREHENSIVE CLINICAL DIAGNOSTIC EVALUATION FOR PEDIATRIC SEVERE APLASTIC ANEMIA 当前儿科严重再生障碍性贫血综合临床诊断评估后的基因检测评估
Pub Date : 2025-11-04 DOI: 10.1016/j.ejcped.2025.100328
Helen D. Reed , Jill L. O. de Jong , Melissa Gaviria , Ashwin Koppayi , Youssef Ahmed , Ian Atkinson , Margret Joos , Maggie Malsch , Matthew McClung , Peter Nicholas , Mancy Shah , Erin E. Sullivan , Hongbo Xie , Silvia Zavarella , Yu Zhou , Barry Zorman , Lucy A. Godley , Taizo A. Nakano , Timothy S. Olson , Alison A. Bertuch , Akiko Shimamura
{"title":"ASSESSMENT OF GENETIC TESTING FOLLOWING CURRENT COMPREHENSIVE CLINICAL DIAGNOSTIC EVALUATION FOR PEDIATRIC SEVERE APLASTIC ANEMIA","authors":"Helen D. Reed , Jill L. O. de Jong , Melissa Gaviria , Ashwin Koppayi , Youssef Ahmed , Ian Atkinson , Margret Joos , Maggie Malsch , Matthew McClung , Peter Nicholas , Mancy Shah , Erin E. Sullivan , Hongbo Xie , Silvia Zavarella , Yu Zhou , Barry Zorman , Lucy A. Godley , Taizo A. Nakano , Timothy S. Olson , Alison A. Bertuch , Akiko Shimamura","doi":"10.1016/j.ejcped.2025.100328","DOIUrl":"10.1016/j.ejcped.2025.100328","url":null,"abstract":"","PeriodicalId":94314,"journal":{"name":"EJC paediatric oncology","volume":"6 ","pages":"Article 100328"},"PeriodicalIF":0.0,"publicationDate":"2025-11-04","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"145428504","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
引用次数: 0
IN-VIVO MOUSE MODEL OF ACUTE MYELOID LEUKEMIA DEVELOPMENT IN CONGENITAL NEUTROPENIA 先天性中性粒细胞减少症急性髓性白血病发展的小鼠体内模型
Pub Date : 2025-11-04 DOI: 10.1016/j.ejcped.2025.100333
Jérémy Haaf, Malte Ritter, Patricia Arreba-Tutusaus, Siarhei Kandabarau, Maksim Klimiankou, Julia Skokowa
{"title":"IN-VIVO MOUSE MODEL OF ACUTE MYELOID LEUKEMIA DEVELOPMENT IN CONGENITAL NEUTROPENIA","authors":"Jérémy Haaf, Malte Ritter, Patricia Arreba-Tutusaus, Siarhei Kandabarau, Maksim Klimiankou, Julia Skokowa","doi":"10.1016/j.ejcped.2025.100333","DOIUrl":"10.1016/j.ejcped.2025.100333","url":null,"abstract":"","PeriodicalId":94314,"journal":{"name":"EJC paediatric oncology","volume":"6 ","pages":"Article 100333"},"PeriodicalIF":0.0,"publicationDate":"2025-11-04","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"145428509","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
引用次数: 0
MITOTIC DEFECTS IMPAIRED CD34+ PROLIFERATION IN GATA2 DEFICIENCY 有丝分裂缺陷损害了gata2缺乏时cd34 +的增殖
Pub Date : 2025-11-04 DOI: 10.1016/j.ejcped.2025.100335
Maria Magallon-Mosella , Damia Romero-Moya , Cristina Calvo , Joan Pera , Eric Torralba-Sales , Miriam Erlacher , Òscar Molina , Alessandra Giorgetti
{"title":"MITOTIC DEFECTS IMPAIRED CD34+ PROLIFERATION IN GATA2 DEFICIENCY","authors":"Maria Magallon-Mosella , Damia Romero-Moya , Cristina Calvo , Joan Pera , Eric Torralba-Sales , Miriam Erlacher , Òscar Molina , Alessandra Giorgetti","doi":"10.1016/j.ejcped.2025.100335","DOIUrl":"10.1016/j.ejcped.2025.100335","url":null,"abstract":"","PeriodicalId":94314,"journal":{"name":"EJC paediatric oncology","volume":"6 ","pages":"Article 100335"},"PeriodicalIF":0.0,"publicationDate":"2025-11-04","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"145428525","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
引用次数: 0
BH3-MIMETIC TREATMENT REVEALS SUBTYPE-SPECIFIC BCL-2 PROTEIN DEPENDENCY IN PEDIATRIC MDS WITH EXCESS BLASTS 模拟bh3治疗揭示了小儿MDS细胞过多的亚型特异性bcl-2蛋白依赖性
Pub Date : 2025-11-04 DOI: 10.1016/j.ejcped.2025.100355
Sheila Bohler , Ayami Yoshimi Nöllke , Nastassja Scheidegger , Ben Haladik , Beat Bornhauser , Michael N. Dworzak , Kaan Boztug , Markus Schmugge , Charlotte M. Niemeyer , Miriam Erlacher
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引用次数: 0
STRATUS PRIMETM A GMP COMPLIANT PROCESS TO CREATE HIGH NUMBERS OF HLA COMPATIBLE DEFINITIVE HSPCS FROM IPSCS USING PIEZO1 AGONISTS Stratus primetm是一个符合GMP的流程,使用piezo1激动剂从ipscs中创建大量hla兼容的最终HSPCS
Pub Date : 2025-11-04 DOI: 10.1016/j.ejcped.2025.100356
Michael P. Cooke , Aayudh Das , Gurinder Singh , Zhi-Jian Liu , Qiao Lin , Sita Karan Patel , Jack Li , Vijaya G. Tirunagaru
{"title":"STRATUS PRIMETM A GMP COMPLIANT PROCESS TO CREATE HIGH NUMBERS OF HLA COMPATIBLE DEFINITIVE HSPCS FROM IPSCS USING PIEZO1 AGONISTS","authors":"Michael P. Cooke , Aayudh Das , Gurinder Singh , Zhi-Jian Liu , Qiao Lin , Sita Karan Patel , Jack Li , Vijaya G. Tirunagaru","doi":"10.1016/j.ejcped.2025.100356","DOIUrl":"10.1016/j.ejcped.2025.100356","url":null,"abstract":"","PeriodicalId":94314,"journal":{"name":"EJC paediatric oncology","volume":"6 ","pages":"Article 100356"},"PeriodicalIF":0.0,"publicationDate":"2025-11-04","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"145428529","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
引用次数: 0
期刊
EJC paediatric oncology
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