Pub Date : 2021-09-05DOI: 10.1183/13993003.congress-2021.pa2098
C. Kim, Christopher Lee, R. Zahigian, N. Nair, A. Sewall, A. Elbert
{"title":"Real-world effects of lumacaftor/ivacaftor (LUM/IVA) in people with cystic fibrosis (pwCF): interim results of a long-term safety study using US CF Foundation Patient Registry (CFFPR) data","authors":"C. Kim, Christopher Lee, R. Zahigian, N. Nair, A. Sewall, A. Elbert","doi":"10.1183/13993003.congress-2021.pa2098","DOIUrl":"https://doi.org/10.1183/13993003.congress-2021.pa2098","url":null,"abstract":"","PeriodicalId":307768,"journal":{"name":"Paediatric cystic fibrosis (CF)","volume":"58 1","pages":"0"},"PeriodicalIF":0.0,"publicationDate":"2021-09-05","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"131932479","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
Pub Date : 2021-09-05DOI: 10.1183/13993003.congress-2021.pa3379
K. Walicka-Serzysko, M. Postek, J. Milczewska, N. Jeneralska, A. Cichocka, E. Siedlecka, L. Morin, Dorotha Sands
{"title":"Late Breaking Abstract - Effects of a new airway clearance technology in children with cystic fibrosis - A homecare randomized controlled trial","authors":"K. Walicka-Serzysko, M. Postek, J. Milczewska, N. Jeneralska, A. Cichocka, E. Siedlecka, L. Morin, Dorotha Sands","doi":"10.1183/13993003.congress-2021.pa3379","DOIUrl":"https://doi.org/10.1183/13993003.congress-2021.pa3379","url":null,"abstract":"","PeriodicalId":307768,"journal":{"name":"Paediatric cystic fibrosis (CF)","volume":"1 1","pages":"0"},"PeriodicalIF":0.0,"publicationDate":"2021-09-05","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"131289102","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
Pub Date : 2021-09-05DOI: 10.1183/13993003.congress-2021.oa2675
C. Willers, B. Frauchiger, E. Stranzinger, G. Bauman, O. Pusterla, O. Bieri, K. Ramsey, P. Latzin
{"title":"Change in functional lung MRI and multiple breath washout outcomes over one year in children with cystic fibrosis","authors":"C. Willers, B. Frauchiger, E. Stranzinger, G. Bauman, O. Pusterla, O. Bieri, K. Ramsey, P. Latzin","doi":"10.1183/13993003.congress-2021.oa2675","DOIUrl":"https://doi.org/10.1183/13993003.congress-2021.oa2675","url":null,"abstract":"","PeriodicalId":307768,"journal":{"name":"Paediatric cystic fibrosis (CF)","volume":"68 2 1","pages":"0"},"PeriodicalIF":0.0,"publicationDate":"2021-09-05","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"131483726","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}