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Molecular Therapy: the Journal of the American Society of Gene Therapy最新文献

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Research Highlights. 研究突出了。
Pub Date : 2020-07-08 DOI: 10.1016/j.ymthe.2020.06.019
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引用次数: 0
In This Issue. 在本期中。
Pub Date : 2020-06-03 DOI: 10.1016/j.ymthe.2020.05.006
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引用次数: 0
Research Highlights. 研究突出了。
Pub Date : 2020-06-03 DOI: 10.1016/j.ymthe.2020.05.008
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引用次数: 0
Family Highlights. 家庭的亮点。
Pub Date : 2020-06-01 DOI: 10.1016/j.ymthe.2020.05.009
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引用次数: 0
Tryptophanyl-tRNA Synthetase, a Novel Damage-Induced Cytokine, Significantly Increases the Therapeutic Effects of Endometrial Stem Cells. 新型损伤诱导细胞因子色氨酸trna合成酶可显著提高子宫内膜干细胞的治疗效果。
Pub Date : 2020-05-01 DOI: 10.1016/j.jcyt.2020.03.171
Se-Ra Park, Soo-Rim Kim, J. Im, Soyi Lim, I. Hong
{"title":"Tryptophanyl-tRNA Synthetase, a Novel Damage-Induced Cytokine, Significantly Increases the Therapeutic Effects of Endometrial Stem Cells.","authors":"Se-Ra Park, Soo-Rim Kim, J. Im, Soyi Lim, I. Hong","doi":"10.1016/j.jcyt.2020.03.171","DOIUrl":"https://doi.org/10.1016/j.jcyt.2020.03.171","url":null,"abstract":"","PeriodicalId":19039,"journal":{"name":"Molecular Therapy: the Journal of the American Society of Gene Therapy","volume":"100 1","pages":""},"PeriodicalIF":0.0,"publicationDate":"2020-05-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"83469246","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
引用次数: 5
MicroRNA 223 3p Negatively Regulates the NLRP3 Inflammasome in Acute and Chronic Liver Injury. MicroRNA 223 3p负调控NLRP3炎性体在急慢性肝损伤中的作用
Pub Date : 2020-02-01 DOI: 10.1016/j.ymthe.2019.09.013
Carolina Jiménez Calvente, Hana Del Pilar, Masahiko Tameda, Casey D. Johnson, A. Feldstein
{"title":"MicroRNA 223 3p Negatively Regulates the NLRP3 Inflammasome in Acute and Chronic Liver Injury.","authors":"Carolina Jiménez Calvente, Hana Del Pilar, Masahiko Tameda, Casey D. Johnson, A. Feldstein","doi":"10.1016/j.ymthe.2019.09.013","DOIUrl":"https://doi.org/10.1016/j.ymthe.2019.09.013","url":null,"abstract":"","PeriodicalId":19039,"journal":{"name":"Molecular Therapy: the Journal of the American Society of Gene Therapy","volume":"13 1","pages":""},"PeriodicalIF":0.0,"publicationDate":"2020-02-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"76623329","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
引用次数: 77
Non-transmissible MV Vector with Segmented RNA Genome Establishes Different Types of iPSCs from Hematopoietic Cells. 利用分段RNA基因组的非传播MV载体从造血细胞中构建不同类型的iPSCs。
Pub Date : 2020-01-01 DOI: 10.1016/j.ymthe.2019.09.007
Takafumi Hiramoto, Maino Tahara, Jiyuan Liao, Y. Soda, Yoshie Miura, R. Kurita, H. Hamana, Kota Inoue, H. Kohara, S. Miyamoto, Y. Hijikata, S. Okano, Y. Yamaguchi, Y. Oda, K. Ichiyanagi, Hidehiro Toh, H. Sasaki, H. Kishi, A. Ryo, A. Muraguchi, M. Takeda, K. Tani
{"title":"Non-transmissible MV Vector with Segmented RNA Genome Establishes Different Types of iPSCs from Hematopoietic Cells.","authors":"Takafumi Hiramoto, Maino Tahara, Jiyuan Liao, Y. Soda, Yoshie Miura, R. Kurita, H. Hamana, Kota Inoue, H. Kohara, S. Miyamoto, Y. Hijikata, S. Okano, Y. Yamaguchi, Y. Oda, K. Ichiyanagi, Hidehiro Toh, H. Sasaki, H. Kishi, A. Ryo, A. Muraguchi, M. Takeda, K. Tani","doi":"10.1016/j.ymthe.2019.09.007","DOIUrl":"https://doi.org/10.1016/j.ymthe.2019.09.007","url":null,"abstract":"","PeriodicalId":19039,"journal":{"name":"Molecular Therapy: the Journal of the American Society of Gene Therapy","volume":"114 1","pages":""},"PeriodicalIF":0.0,"publicationDate":"2020-01-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"79336154","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
引用次数: 7
Simultaneous Deletion of Endogenous TCRαβ for TCR Gene Therapy Creates an Improved and Safe Cellular Therapeutic. 同时删除内源性TCRαβ用于TCR基因治疗创造了一种改进和安全的细胞治疗方法。
Pub Date : 2020-01-01 DOI: 10.1016/j.ymthe.2019.10.001
Laura T Morton, Rogier M. Reijmers, A. Wouters, C. Kweekel, D. Remst, C. R. Pothast, J. Falkenburg, M. Heemskerk
{"title":"Simultaneous Deletion of Endogenous TCRαβ for TCR Gene Therapy Creates an Improved and Safe Cellular Therapeutic.","authors":"Laura T Morton, Rogier M. Reijmers, A. Wouters, C. Kweekel, D. Remst, C. R. Pothast, J. Falkenburg, M. Heemskerk","doi":"10.1016/j.ymthe.2019.10.001","DOIUrl":"https://doi.org/10.1016/j.ymthe.2019.10.001","url":null,"abstract":"","PeriodicalId":19039,"journal":{"name":"Molecular Therapy: the Journal of the American Society of Gene Therapy","volume":"378 1","pages":""},"PeriodicalIF":0.0,"publicationDate":"2020-01-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"76527714","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
引用次数: 44
Long-Term Structural Outcomes of Late-Stage RPE65 Gene Therapy. 晚期RPE65基因治疗的长期结构结果。
Pub Date : 2020-01-01 DOI: 10.1016/j.ymthe.2019.08.013
Kristin L. Gardiner, A. Cideciyan, M. Świder, V. Dufour, A. Sumaroka, A. Komáromy, W. Hauswirth, S. Iwabe, S. Jacobson, W. Beltran, G. Aguirre
{"title":"Long-Term Structural Outcomes of Late-Stage RPE65 Gene Therapy.","authors":"Kristin L. Gardiner, A. Cideciyan, M. Świder, V. Dufour, A. Sumaroka, A. Komáromy, W. Hauswirth, S. Iwabe, S. Jacobson, W. Beltran, G. Aguirre","doi":"10.1016/j.ymthe.2019.08.013","DOIUrl":"https://doi.org/10.1016/j.ymthe.2019.08.013","url":null,"abstract":"","PeriodicalId":19039,"journal":{"name":"Molecular Therapy: the Journal of the American Society of Gene Therapy","volume":"3 1","pages":""},"PeriodicalIF":0.0,"publicationDate":"2020-01-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"88445956","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
引用次数: 48
A Trans-amplifying RNA Vaccine Strategy for Induction of Potent Protective Immunity. 一种诱导强保护性免疫的反式扩增RNA疫苗策略
Pub Date : 2020-01-01 DOI: 10.1016/j.ymthe.2019.09.009
T. Beissert, Mario Perković, Annette B. Vogel, Stephanie Erbar, Kerstin C. Walzer, Tina Hempel, S. Brill, Erik S. Haefner, René Becker, Ö. Türeci, U. Şahin
{"title":"A Trans-amplifying RNA Vaccine Strategy for Induction of Potent Protective Immunity.","authors":"T. Beissert, Mario Perković, Annette B. Vogel, Stephanie Erbar, Kerstin C. Walzer, Tina Hempel, S. Brill, Erik S. Haefner, René Becker, Ö. Türeci, U. Şahin","doi":"10.1016/j.ymthe.2019.09.009","DOIUrl":"https://doi.org/10.1016/j.ymthe.2019.09.009","url":null,"abstract":"","PeriodicalId":19039,"journal":{"name":"Molecular Therapy: the Journal of the American Society of Gene Therapy","volume":"6 1","pages":""},"PeriodicalIF":0.0,"publicationDate":"2020-01-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"77703321","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
引用次数: 85
期刊
Molecular Therapy: the Journal of the American Society of Gene Therapy
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