Pub Date : 2020-07-08DOI: 10.1016/j.ymthe.2020.06.019
{"title":"Research Highlights.","authors":"","doi":"10.1016/j.ymthe.2020.06.019","DOIUrl":"https://doi.org/10.1016/j.ymthe.2020.06.019","url":null,"abstract":"","PeriodicalId":19039,"journal":{"name":"Molecular Therapy: the Journal of the American Society of Gene Therapy","volume":"20 1","pages":"1552-1554"},"PeriodicalIF":0.0,"publicationDate":"2020-07-08","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"76337543","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
Pub Date : 2020-06-03DOI: 10.1016/j.ymthe.2020.05.006
{"title":"In This Issue.","authors":"","doi":"10.1016/j.ymthe.2020.05.006","DOIUrl":"https://doi.org/10.1016/j.ymthe.2020.05.006","url":null,"abstract":"","PeriodicalId":19039,"journal":{"name":"Molecular Therapy: the Journal of the American Society of Gene Therapy","volume":"52 1","pages":"1383"},"PeriodicalIF":0.0,"publicationDate":"2020-06-03","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"75311342","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
Pub Date : 2020-06-03DOI: 10.1016/j.ymthe.2020.05.008
{"title":"Research Highlights.","authors":"","doi":"10.1016/j.ymthe.2020.05.008","DOIUrl":"https://doi.org/10.1016/j.ymthe.2020.05.008","url":null,"abstract":"","PeriodicalId":19039,"journal":{"name":"Molecular Therapy: the Journal of the American Society of Gene Therapy","volume":"36 1","pages":"1385-1386"},"PeriodicalIF":0.0,"publicationDate":"2020-06-03","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"75497274","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
Pub Date : 2020-06-01DOI: 10.1016/j.ymthe.2020.05.009
{"title":"Family Highlights.","authors":"","doi":"10.1016/j.ymthe.2020.05.009","DOIUrl":"https://doi.org/10.1016/j.ymthe.2020.05.009","url":null,"abstract":"","PeriodicalId":19039,"journal":{"name":"Molecular Therapy: the Journal of the American Society of Gene Therapy","volume":"19 1","pages":"1384"},"PeriodicalIF":0.0,"publicationDate":"2020-06-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"90902261","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
Pub Date : 2020-05-01DOI: 10.1016/j.jcyt.2020.03.171
Se-Ra Park, Soo-Rim Kim, J. Im, Soyi Lim, I. Hong
{"title":"Tryptophanyl-tRNA Synthetase, a Novel Damage-Induced Cytokine, Significantly Increases the Therapeutic Effects of Endometrial Stem Cells.","authors":"Se-Ra Park, Soo-Rim Kim, J. Im, Soyi Lim, I. Hong","doi":"10.1016/j.jcyt.2020.03.171","DOIUrl":"https://doi.org/10.1016/j.jcyt.2020.03.171","url":null,"abstract":"","PeriodicalId":19039,"journal":{"name":"Molecular Therapy: the Journal of the American Society of Gene Therapy","volume":"100 1","pages":""},"PeriodicalIF":0.0,"publicationDate":"2020-05-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"83469246","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
Pub Date : 2020-02-01DOI: 10.1016/j.ymthe.2019.09.013
Carolina Jiménez Calvente, Hana Del Pilar, Masahiko Tameda, Casey D. Johnson, A. Feldstein
{"title":"MicroRNA 223 3p Negatively Regulates the NLRP3 Inflammasome in Acute and Chronic Liver Injury.","authors":"Carolina Jiménez Calvente, Hana Del Pilar, Masahiko Tameda, Casey D. Johnson, A. Feldstein","doi":"10.1016/j.ymthe.2019.09.013","DOIUrl":"https://doi.org/10.1016/j.ymthe.2019.09.013","url":null,"abstract":"","PeriodicalId":19039,"journal":{"name":"Molecular Therapy: the Journal of the American Society of Gene Therapy","volume":"13 1","pages":""},"PeriodicalIF":0.0,"publicationDate":"2020-02-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"76623329","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
Pub Date : 2020-01-01DOI: 10.1016/j.ymthe.2019.09.007
Takafumi Hiramoto, Maino Tahara, Jiyuan Liao, Y. Soda, Yoshie Miura, R. Kurita, H. Hamana, Kota Inoue, H. Kohara, S. Miyamoto, Y. Hijikata, S. Okano, Y. Yamaguchi, Y. Oda, K. Ichiyanagi, Hidehiro Toh, H. Sasaki, H. Kishi, A. Ryo, A. Muraguchi, M. Takeda, K. Tani
{"title":"Non-transmissible MV Vector with Segmented RNA Genome Establishes Different Types of iPSCs from Hematopoietic Cells.","authors":"Takafumi Hiramoto, Maino Tahara, Jiyuan Liao, Y. Soda, Yoshie Miura, R. Kurita, H. Hamana, Kota Inoue, H. Kohara, S. Miyamoto, Y. Hijikata, S. Okano, Y. Yamaguchi, Y. Oda, K. Ichiyanagi, Hidehiro Toh, H. Sasaki, H. Kishi, A. Ryo, A. Muraguchi, M. Takeda, K. Tani","doi":"10.1016/j.ymthe.2019.09.007","DOIUrl":"https://doi.org/10.1016/j.ymthe.2019.09.007","url":null,"abstract":"","PeriodicalId":19039,"journal":{"name":"Molecular Therapy: the Journal of the American Society of Gene Therapy","volume":"114 1","pages":""},"PeriodicalIF":0.0,"publicationDate":"2020-01-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"79336154","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
Pub Date : 2020-01-01DOI: 10.1016/j.ymthe.2019.10.001
Laura T Morton, Rogier M. Reijmers, A. Wouters, C. Kweekel, D. Remst, C. R. Pothast, J. Falkenburg, M. Heemskerk
{"title":"Simultaneous Deletion of Endogenous TCRαβ for TCR Gene Therapy Creates an Improved and Safe Cellular Therapeutic.","authors":"Laura T Morton, Rogier M. Reijmers, A. Wouters, C. Kweekel, D. Remst, C. R. Pothast, J. Falkenburg, M. Heemskerk","doi":"10.1016/j.ymthe.2019.10.001","DOIUrl":"https://doi.org/10.1016/j.ymthe.2019.10.001","url":null,"abstract":"","PeriodicalId":19039,"journal":{"name":"Molecular Therapy: the Journal of the American Society of Gene Therapy","volume":"378 1","pages":""},"PeriodicalIF":0.0,"publicationDate":"2020-01-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"76527714","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
Pub Date : 2020-01-01DOI: 10.1016/j.ymthe.2019.08.013
Kristin L. Gardiner, A. Cideciyan, M. Świder, V. Dufour, A. Sumaroka, A. Komáromy, W. Hauswirth, S. Iwabe, S. Jacobson, W. Beltran, G. Aguirre
{"title":"Long-Term Structural Outcomes of Late-Stage RPE65 Gene Therapy.","authors":"Kristin L. Gardiner, A. Cideciyan, M. Świder, V. Dufour, A. Sumaroka, A. Komáromy, W. Hauswirth, S. Iwabe, S. Jacobson, W. Beltran, G. Aguirre","doi":"10.1016/j.ymthe.2019.08.013","DOIUrl":"https://doi.org/10.1016/j.ymthe.2019.08.013","url":null,"abstract":"","PeriodicalId":19039,"journal":{"name":"Molecular Therapy: the Journal of the American Society of Gene Therapy","volume":"3 1","pages":""},"PeriodicalIF":0.0,"publicationDate":"2020-01-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"88445956","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
Pub Date : 2020-01-01DOI: 10.1016/j.ymthe.2019.09.009
T. Beissert, Mario Perković, Annette B. Vogel, Stephanie Erbar, Kerstin C. Walzer, Tina Hempel, S. Brill, Erik S. Haefner, René Becker, Ö. Türeci, U. Şahin
{"title":"A Trans-amplifying RNA Vaccine Strategy for Induction of Potent Protective Immunity.","authors":"T. Beissert, Mario Perković, Annette B. Vogel, Stephanie Erbar, Kerstin C. Walzer, Tina Hempel, S. Brill, Erik S. Haefner, René Becker, Ö. Türeci, U. Şahin","doi":"10.1016/j.ymthe.2019.09.009","DOIUrl":"https://doi.org/10.1016/j.ymthe.2019.09.009","url":null,"abstract":"","PeriodicalId":19039,"journal":{"name":"Molecular Therapy: the Journal of the American Society of Gene Therapy","volume":"6 1","pages":""},"PeriodicalIF":0.0,"publicationDate":"2020-01-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"77703321","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}