Pub Date : 2017-02-01DOI: 10.1016/j.ymthe.2017.01.002
G. Santilli, A. Thrasher
{"title":"A New Chapter on Targeted Gene Insertion for X-CGD: Do Not Skip the Intro(n).","authors":"G. Santilli, A. Thrasher","doi":"10.1016/j.ymthe.2017.01.002","DOIUrl":"https://doi.org/10.1016/j.ymthe.2017.01.002","url":null,"abstract":"","PeriodicalId":19039,"journal":{"name":"Molecular Therapy: the Journal of the American Society of Gene Therapy","volume":"4 1","pages":"307-309"},"PeriodicalIF":0.0,"publicationDate":"2017-02-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"76339611","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
Pub Date : 2017-02-01DOI: 10.1016/j.ymthe.2016.11.002
A. Karageorgis, M. Claron, R. Jugé, C. Aspord, Fabien Thoreau, C. Leloup, J. Kucharczak, J. Plumas, M. Henry, A. Hurbin, P. Verdié, Jean Martínez, G. Subra, P. Dumy, D. Boturyn, A. Aouacheria, J. Coll
{"title":"Systemic Delivery of Tumor-Targeted Bax-Derived Membrane-Active Peptides for the Treatment of Melanoma Tumors in a Humanized SCID Mouse Model.","authors":"A. Karageorgis, M. Claron, R. Jugé, C. Aspord, Fabien Thoreau, C. Leloup, J. Kucharczak, J. Plumas, M. Henry, A. Hurbin, P. Verdié, Jean Martínez, G. Subra, P. Dumy, D. Boturyn, A. Aouacheria, J. Coll","doi":"10.1016/j.ymthe.2016.11.002","DOIUrl":"https://doi.org/10.1016/j.ymthe.2016.11.002","url":null,"abstract":"","PeriodicalId":19039,"journal":{"name":"Molecular Therapy: the Journal of the American Society of Gene Therapy","volume":"26 1","pages":"534-546"},"PeriodicalIF":0.0,"publicationDate":"2017-02-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"81378734","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
Pub Date : 2017-02-01DOI: 10.1016/j.ymthe.2017.01.001
R. Hardet, F. Mingozzi
{"title":"Oral Tolerance: Another Reason to Eat Your Veggies!","authors":"R. Hardet, F. Mingozzi","doi":"10.1016/j.ymthe.2017.01.001","DOIUrl":"https://doi.org/10.1016/j.ymthe.2017.01.001","url":null,"abstract":"","PeriodicalId":19039,"journal":{"name":"Molecular Therapy: the Journal of the American Society of Gene Therapy","volume":"15 1","pages":"311-313"},"PeriodicalIF":0.0,"publicationDate":"2017-02-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"79560419","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
Pub Date : 2017-02-01DOI: 10.1016/j.ymthe.2016.11.013
Jiusheng Deng, Yanqiu Li, A. Pennati, S. Yuan, Jian Hui Wu, E. Waller, J. Galipeau
{"title":"GM-CSF and IL-4 Fusion Cytokine Induces B Cell-Dependent Hematopoietic Regeneration.","authors":"Jiusheng Deng, Yanqiu Li, A. Pennati, S. Yuan, Jian Hui Wu, E. Waller, J. Galipeau","doi":"10.1016/j.ymthe.2016.11.013","DOIUrl":"https://doi.org/10.1016/j.ymthe.2016.11.013","url":null,"abstract":"","PeriodicalId":19039,"journal":{"name":"Molecular Therapy: the Journal of the American Society of Gene Therapy","volume":"46 1","pages":"416-426"},"PeriodicalIF":0.0,"publicationDate":"2017-02-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"74192425","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
Pub Date : 2017-02-01DOI: 10.1016/j.ymthe.2016.11.017
Felipe Cabral-Miranda, Elisa Nicoloso-Simões, J. Adão-Novaes, V. Chiodo, W. Hauswirth, R. Linden, L. B. Chiarini, H. Petrs-Silva
{"title":"rAAV8-733-Mediated Gene Transfer of CHIP/Stub-1 Prevents Hippocampal Neuronal Death in Experimental Brain Ischemia.","authors":"Felipe Cabral-Miranda, Elisa Nicoloso-Simões, J. Adão-Novaes, V. Chiodo, W. Hauswirth, R. Linden, L. B. Chiarini, H. Petrs-Silva","doi":"10.1016/j.ymthe.2016.11.017","DOIUrl":"https://doi.org/10.1016/j.ymthe.2016.11.017","url":null,"abstract":"","PeriodicalId":19039,"journal":{"name":"Molecular Therapy: the Journal of the American Society of Gene Therapy","volume":"9 1","pages":"392-400"},"PeriodicalIF":0.0,"publicationDate":"2017-02-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"85653480","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
Pub Date : 2017-02-01DOI: 10.1016/j.ymthe.2016.12.008
Y. Zhang, Xing Li, B. Ciric, Cun-Gen Ma, B. Gran, A. Rostami, Guang-Xian Zhang
{"title":"Effect of Fingolimod on Neural Stem Cells: A Novel Mechanism and Broadened Application for Neural Repair.","authors":"Y. Zhang, Xing Li, B. Ciric, Cun-Gen Ma, B. Gran, A. Rostami, Guang-Xian Zhang","doi":"10.1016/j.ymthe.2016.12.008","DOIUrl":"https://doi.org/10.1016/j.ymthe.2016.12.008","url":null,"abstract":"","PeriodicalId":19039,"journal":{"name":"Molecular Therapy: the Journal of the American Society of Gene Therapy","volume":"51 1","pages":"401-415"},"PeriodicalIF":0.0,"publicationDate":"2017-02-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"82252854","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
Pub Date : 2017-02-01DOI: 10.1016/j.ymthe.2016.11.019
Yongmin Yan, Wenqiang Jiang, Youwen Tan, S. Zou, Hongguang Zhang, F. Mao, A. Gong, H. Qian, Wenrong Xu
{"title":"hucMSC Exosome-Derived GPX1 Is Required for the Recovery of Hepatic Oxidant Injury.","authors":"Yongmin Yan, Wenqiang Jiang, Youwen Tan, S. Zou, Hongguang Zhang, F. Mao, A. Gong, H. Qian, Wenrong Xu","doi":"10.1016/j.ymthe.2016.11.019","DOIUrl":"https://doi.org/10.1016/j.ymthe.2016.11.019","url":null,"abstract":"","PeriodicalId":19039,"journal":{"name":"Molecular Therapy: the Journal of the American Society of Gene Therapy","volume":"51 1","pages":"465-479"},"PeriodicalIF":0.0,"publicationDate":"2017-02-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"75018983","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
Pub Date : 2017-02-01DOI: 10.1016/j.ymthe.2016.11.008
Shuai Xue, Jianli Yin, Jiawei Shao, Yuanhuan Yu, Linfeng Yang, Yidan Wang, Mingqi Xie, M. Fussenegger, Haifeng Ye
{"title":"A Synthetic-Biology-Inspired Therapeutic Strategy for Targeting and Treating Hepatogenous Diabetes.","authors":"Shuai Xue, Jianli Yin, Jiawei Shao, Yuanhuan Yu, Linfeng Yang, Yidan Wang, Mingqi Xie, M. Fussenegger, Haifeng Ye","doi":"10.1016/j.ymthe.2016.11.008","DOIUrl":"https://doi.org/10.1016/j.ymthe.2016.11.008","url":null,"abstract":"","PeriodicalId":19039,"journal":{"name":"Molecular Therapy: the Journal of the American Society of Gene Therapy","volume":"50 1","pages":"443-455"},"PeriodicalIF":0.0,"publicationDate":"2017-02-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"85679367","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
Pub Date : 2017-02-01DOI: 10.1016/j.ymthe.2016.12.010
B. György, C. Sage, Artur A. Indzhykulian, D. Scheffer, A. Brisson, Sisareuth Tan, Xudong Wu, Adrienn Volak, D. Mu, Panos I. Tamvakologos, Yaqiao Li, Z. Fitzpatrick, M. Ericsson, X. Breakefield, D. Corey, C. Maguire
{"title":"Rescue of Hearing by Gene Delivery to Inner-Ear Hair Cells Using Exosome-Associated AAV.","authors":"B. György, C. Sage, Artur A. Indzhykulian, D. Scheffer, A. Brisson, Sisareuth Tan, Xudong Wu, Adrienn Volak, D. Mu, Panos I. Tamvakologos, Yaqiao Li, Z. Fitzpatrick, M. Ericsson, X. Breakefield, D. Corey, C. Maguire","doi":"10.1016/j.ymthe.2016.12.010","DOIUrl":"https://doi.org/10.1016/j.ymthe.2016.12.010","url":null,"abstract":"","PeriodicalId":19039,"journal":{"name":"Molecular Therapy: the Journal of the American Society of Gene Therapy","volume":"7 1","pages":"379-391"},"PeriodicalIF":0.0,"publicationDate":"2017-02-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"74229410","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
Pub Date : 2017-02-01DOI: 10.1016/j.ymthe.2016.12.007
S. Fishman, M. Lewis, L. K. Siew, E. de Leenheer, Dimitri Kakabadse, Joanne Davies, Doron Ziv, A. Margalit, N. Karin, G. Gross, F. Wong
{"title":"Adoptive Transfer of mRNA-Transfected T Cells Redirected against Diabetogenic CD8 T Cells Can Prevent Diabetes.","authors":"S. Fishman, M. Lewis, L. K. Siew, E. de Leenheer, Dimitri Kakabadse, Joanne Davies, Doron Ziv, A. Margalit, N. Karin, G. Gross, F. Wong","doi":"10.1016/j.ymthe.2016.12.007","DOIUrl":"https://doi.org/10.1016/j.ymthe.2016.12.007","url":null,"abstract":"","PeriodicalId":19039,"journal":{"name":"Molecular Therapy: the Journal of the American Society of Gene Therapy","volume":"32 1","pages":"456-464"},"PeriodicalIF":0.0,"publicationDate":"2017-02-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"86819575","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}