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Molecular Therapy: the Journal of the American Society of Gene Therapy最新文献

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A New Chapter on Targeted Gene Insertion for X-CGD: Do Not Skip the Intro(n). 关于X-CGD靶向基因插入的新章:不要跳过引言(n)。
Pub Date : 2017-02-01 DOI: 10.1016/j.ymthe.2017.01.002
G. Santilli, A. Thrasher
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引用次数: 3
Systemic Delivery of Tumor-Targeted Bax-Derived Membrane-Active Peptides for the Treatment of Melanoma Tumors in a Humanized SCID Mouse Model. 在人源SCID小鼠模型中,肿瘤靶向bax来源的膜活性肽的全身递送治疗黑色素瘤。
Pub Date : 2017-02-01 DOI: 10.1016/j.ymthe.2016.11.002
A. Karageorgis, M. Claron, R. Jugé, C. Aspord, Fabien Thoreau, C. Leloup, J. Kucharczak, J. Plumas, M. Henry, A. Hurbin, P. Verdié, Jean Martínez, G. Subra, P. Dumy, D. Boturyn, A. Aouacheria, J. Coll
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引用次数: 15
Oral Tolerance: Another Reason to Eat Your Veggies! 口腔耐受:吃蔬菜的另一个原因!
Pub Date : 2017-02-01 DOI: 10.1016/j.ymthe.2017.01.001
R. Hardet, F. Mingozzi
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引用次数: 1
GM-CSF and IL-4 Fusion Cytokine Induces B Cell-Dependent Hematopoietic Regeneration. GM-CSF和IL-4融合细胞因子诱导B细胞依赖性造血再生。
Pub Date : 2017-02-01 DOI: 10.1016/j.ymthe.2016.11.013
Jiusheng Deng, Yanqiu Li, A. Pennati, S. Yuan, Jian Hui Wu, E. Waller, J. Galipeau
{"title":"GM-CSF and IL-4 Fusion Cytokine Induces B Cell-Dependent Hematopoietic Regeneration.","authors":"Jiusheng Deng, Yanqiu Li, A. Pennati, S. Yuan, Jian Hui Wu, E. Waller, J. Galipeau","doi":"10.1016/j.ymthe.2016.11.013","DOIUrl":"https://doi.org/10.1016/j.ymthe.2016.11.013","url":null,"abstract":"","PeriodicalId":19039,"journal":{"name":"Molecular Therapy: the Journal of the American Society of Gene Therapy","volume":"46 1","pages":"416-426"},"PeriodicalIF":0.0,"publicationDate":"2017-02-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"74192425","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
引用次数: 2
rAAV8-733-Mediated Gene Transfer of CHIP/Stub-1 Prevents Hippocampal Neuronal Death in Experimental Brain Ischemia. raav8 -733介导的CHIP/Stub-1基因转移预防实验性脑缺血海马神经元死亡
Pub Date : 2017-02-01 DOI: 10.1016/j.ymthe.2016.11.017
Felipe Cabral-Miranda, Elisa Nicoloso-Simões, J. Adão-Novaes, V. Chiodo, W. Hauswirth, R. Linden, L. B. Chiarini, H. Petrs-Silva
{"title":"rAAV8-733-Mediated Gene Transfer of CHIP/Stub-1 Prevents Hippocampal Neuronal Death in Experimental Brain Ischemia.","authors":"Felipe Cabral-Miranda, Elisa Nicoloso-Simões, J. Adão-Novaes, V. Chiodo, W. Hauswirth, R. Linden, L. B. Chiarini, H. Petrs-Silva","doi":"10.1016/j.ymthe.2016.11.017","DOIUrl":"https://doi.org/10.1016/j.ymthe.2016.11.017","url":null,"abstract":"","PeriodicalId":19039,"journal":{"name":"Molecular Therapy: the Journal of the American Society of Gene Therapy","volume":"9 1","pages":"392-400"},"PeriodicalIF":0.0,"publicationDate":"2017-02-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"85653480","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
引用次数: 17
Effect of Fingolimod on Neural Stem Cells: A Novel Mechanism and Broadened Application for Neural Repair. 芬戈莫德对神经干细胞的影响:一种新的机制及其在神经修复中的广泛应用。
Pub Date : 2017-02-01 DOI: 10.1016/j.ymthe.2016.12.008
Y. Zhang, Xing Li, B. Ciric, Cun-Gen Ma, B. Gran, A. Rostami, Guang-Xian Zhang
{"title":"Effect of Fingolimod on Neural Stem Cells: A Novel Mechanism and Broadened Application for Neural Repair.","authors":"Y. Zhang, Xing Li, B. Ciric, Cun-Gen Ma, B. Gran, A. Rostami, Guang-Xian Zhang","doi":"10.1016/j.ymthe.2016.12.008","DOIUrl":"https://doi.org/10.1016/j.ymthe.2016.12.008","url":null,"abstract":"","PeriodicalId":19039,"journal":{"name":"Molecular Therapy: the Journal of the American Society of Gene Therapy","volume":"51 1","pages":"401-415"},"PeriodicalIF":0.0,"publicationDate":"2017-02-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"82252854","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
引用次数: 33
hucMSC Exosome-Derived GPX1 Is Required for the Recovery of Hepatic Oxidant Injury. humsc外泌体衍生的GPX1是肝氧化损伤恢复所必需的。
Pub Date : 2017-02-01 DOI: 10.1016/j.ymthe.2016.11.019
Yongmin Yan, Wenqiang Jiang, Youwen Tan, S. Zou, Hongguang Zhang, F. Mao, A. Gong, H. Qian, Wenrong Xu
{"title":"hucMSC Exosome-Derived GPX1 Is Required for the Recovery of Hepatic Oxidant Injury.","authors":"Yongmin Yan, Wenqiang Jiang, Youwen Tan, S. Zou, Hongguang Zhang, F. Mao, A. Gong, H. Qian, Wenrong Xu","doi":"10.1016/j.ymthe.2016.11.019","DOIUrl":"https://doi.org/10.1016/j.ymthe.2016.11.019","url":null,"abstract":"","PeriodicalId":19039,"journal":{"name":"Molecular Therapy: the Journal of the American Society of Gene Therapy","volume":"51 1","pages":"465-479"},"PeriodicalIF":0.0,"publicationDate":"2017-02-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"75018983","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
引用次数: 223
A Synthetic-Biology-Inspired Therapeutic Strategy for Targeting and Treating Hepatogenous Diabetes. 基于合成生物学的肝源性糖尿病靶向治疗策略
Pub Date : 2017-02-01 DOI: 10.1016/j.ymthe.2016.11.008
Shuai Xue, Jianli Yin, Jiawei Shao, Yuanhuan Yu, Linfeng Yang, Yidan Wang, Mingqi Xie, M. Fussenegger, Haifeng Ye
{"title":"A Synthetic-Biology-Inspired Therapeutic Strategy for Targeting and Treating Hepatogenous Diabetes.","authors":"Shuai Xue, Jianli Yin, Jiawei Shao, Yuanhuan Yu, Linfeng Yang, Yidan Wang, Mingqi Xie, M. Fussenegger, Haifeng Ye","doi":"10.1016/j.ymthe.2016.11.008","DOIUrl":"https://doi.org/10.1016/j.ymthe.2016.11.008","url":null,"abstract":"","PeriodicalId":19039,"journal":{"name":"Molecular Therapy: the Journal of the American Society of Gene Therapy","volume":"50 1","pages":"443-455"},"PeriodicalIF":0.0,"publicationDate":"2017-02-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"85679367","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
引用次数: 39
Rescue of Hearing by Gene Delivery to Inner-Ear Hair Cells Using Exosome-Associated AAV. 利用外泌体相关AAV向内耳毛细胞传递基因拯救听力。
Pub Date : 2017-02-01 DOI: 10.1016/j.ymthe.2016.12.010
B. György, C. Sage, Artur A. Indzhykulian, D. Scheffer, A. Brisson, Sisareuth Tan, Xudong Wu, Adrienn Volak, D. Mu, Panos I. Tamvakologos, Yaqiao Li, Z. Fitzpatrick, M. Ericsson, X. Breakefield, D. Corey, C. Maguire
{"title":"Rescue of Hearing by Gene Delivery to Inner-Ear Hair Cells Using Exosome-Associated AAV.","authors":"B. György, C. Sage, Artur A. Indzhykulian, D. Scheffer, A. Brisson, Sisareuth Tan, Xudong Wu, Adrienn Volak, D. Mu, Panos I. Tamvakologos, Yaqiao Li, Z. Fitzpatrick, M. Ericsson, X. Breakefield, D. Corey, C. Maguire","doi":"10.1016/j.ymthe.2016.12.010","DOIUrl":"https://doi.org/10.1016/j.ymthe.2016.12.010","url":null,"abstract":"","PeriodicalId":19039,"journal":{"name":"Molecular Therapy: the Journal of the American Society of Gene Therapy","volume":"7 1","pages":"379-391"},"PeriodicalIF":0.0,"publicationDate":"2017-02-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"74229410","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
引用次数: 169
Adoptive Transfer of mRNA-Transfected T Cells Redirected against Diabetogenic CD8 T Cells Can Prevent Diabetes. 靶向糖尿病性CD8 T细胞的mrna转染T细胞过继转移可预防糖尿病
Pub Date : 2017-02-01 DOI: 10.1016/j.ymthe.2016.12.007
S. Fishman, M. Lewis, L. K. Siew, E. de Leenheer, Dimitri Kakabadse, Joanne Davies, Doron Ziv, A. Margalit, N. Karin, G. Gross, F. Wong
{"title":"Adoptive Transfer of mRNA-Transfected T Cells Redirected against Diabetogenic CD8 T Cells Can Prevent Diabetes.","authors":"S. Fishman, M. Lewis, L. K. Siew, E. de Leenheer, Dimitri Kakabadse, Joanne Davies, Doron Ziv, A. Margalit, N. Karin, G. Gross, F. Wong","doi":"10.1016/j.ymthe.2016.12.007","DOIUrl":"https://doi.org/10.1016/j.ymthe.2016.12.007","url":null,"abstract":"","PeriodicalId":19039,"journal":{"name":"Molecular Therapy: the Journal of the American Society of Gene Therapy","volume":"32 1","pages":"456-464"},"PeriodicalIF":0.0,"publicationDate":"2017-02-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"86819575","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
引用次数: 27
期刊
Molecular Therapy: the Journal of the American Society of Gene Therapy
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