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Molecular Therapy: the Journal of the American Society of Gene Therapy最新文献

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ncRNA-Encoded Peptides or Proteins and Cancer. ncrna编码肽或蛋白质与癌症。
Pub Date : 2019-10-01 DOI: 10.1016/j.ymthe.2019.09.001
Jizhong Wang, Song Zhu, Nan Meng, Yutian He, R. Lu, Guang-Rong Yan
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引用次数: 190
Peripheral Circulating Exosome-Mediated Delivery of miR-155 as a Novel Mechanism for Acute Lung Inflammation. 外周循环外泌体介导的miR-155递送作为急性肺部炎症的新机制。
Pub Date : 2019-10-01 DOI: 10.1016/j.ymthe.2019.07.003
Kangfeng Jiang, Jing Yang, Shuai Guo, Gan Zhao, Haichong Wu, Ganzhen Deng
{"title":"Peripheral Circulating Exosome-Mediated Delivery of miR-155 as a Novel Mechanism for Acute Lung Inflammation.","authors":"Kangfeng Jiang, Jing Yang, Shuai Guo, Gan Zhao, Haichong Wu, Ganzhen Deng","doi":"10.1016/j.ymthe.2019.07.003","DOIUrl":"https://doi.org/10.1016/j.ymthe.2019.07.003","url":null,"abstract":"","PeriodicalId":19039,"journal":{"name":"Molecular Therapy: the Journal of the American Society of Gene Therapy","volume":"37 1","pages":""},"PeriodicalIF":0.0,"publicationDate":"2019-10-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"84038218","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
引用次数: 135
AAV6 Is Superior to Clade F AAVs in Stimulating Homologous Recombination-Based Genome Editing in Human HSPCs. AAV6在促进人类HSPCs同源重组基因组编辑方面优于进化枝F AAVs。
Pub Date : 2019-09-12 DOI: 10.1016/j.ymthe.2019.09.005
Amanda M. Dudek, M. Porteus
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引用次数: 13
Long-Term Safety and Efficacy of Gene-Pulmonary Macrophage Transplantation Therapy of PAP in Csf2ra-/- Mice. 基因-肺巨噬细胞移植治疗Csf2ra-/-小鼠PAP的长期安全性和有效性。
Pub Date : 2019-09-01 DOI: 10.1016/j.ymthe.2019.06.010
P. Arumugam, Takuji Suzuki, K. Shima, C. McCarthy, A. Sallese, M. Wessendarp, Yan Ma, Johann Meyer, D. Black, C. Chalk, B. Carey, N. Lachmann, T. Moritz, B. Trapnell
{"title":"Long-Term Safety and Efficacy of Gene-Pulmonary Macrophage Transplantation Therapy of PAP in Csf2ra-/- Mice.","authors":"P. Arumugam, Takuji Suzuki, K. Shima, C. McCarthy, A. Sallese, M. Wessendarp, Yan Ma, Johann Meyer, D. Black, C. Chalk, B. Carey, N. Lachmann, T. Moritz, B. Trapnell","doi":"10.1016/j.ymthe.2019.06.010","DOIUrl":"https://doi.org/10.1016/j.ymthe.2019.06.010","url":null,"abstract":"","PeriodicalId":19039,"journal":{"name":"Molecular Therapy: the Journal of the American Society of Gene Therapy","volume":"28 1","pages":""},"PeriodicalIF":0.0,"publicationDate":"2019-09-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"76785254","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
引用次数: 12
The Delivery of a Wnt Pathway Inhibitor Toward CSCs Requires Stable Liposome Encapsulation and Delayed Drug Release in Tumor Tissues. 向CSCs递送Wnt通路抑制剂需要稳定的脂质体包封和延迟药物在肿瘤组织中的释放。
Pub Date : 2019-09-01 DOI: 10.1016/J.YMTHE.2019.06.013
Chong Li, Yaoyao Liang, Jing Cao, Ning Zhang, Xiaohui Wei, Meiqing Tu, Fengwei Xu, Yuhong Xu
{"title":"The Delivery of a Wnt Pathway Inhibitor Toward CSCs Requires Stable Liposome Encapsulation and Delayed Drug Release in Tumor Tissues.","authors":"Chong Li, Yaoyao Liang, Jing Cao, Ning Zhang, Xiaohui Wei, Meiqing Tu, Fengwei Xu, Yuhong Xu","doi":"10.1016/J.YMTHE.2019.06.013","DOIUrl":"https://doi.org/10.1016/J.YMTHE.2019.06.013","url":null,"abstract":"","PeriodicalId":19039,"journal":{"name":"Molecular Therapy: the Journal of the American Society of Gene Therapy","volume":"29 1","pages":""},"PeriodicalIF":0.0,"publicationDate":"2019-09-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"76636540","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
引用次数: 15
Circular RNAs: A Novel Class of Functional RNA Molecules with a Therapeutic Perspective. 环状RNA:一类具有治疗前景的新型功能性RNA分子。
Pub Date : 2019-08-01 DOI: 10.1016/j.ymthe.2019.07.001
L. Santer, C. Bär, T. Thum
{"title":"Circular RNAs: A Novel Class of Functional RNA Molecules with a Therapeutic Perspective.","authors":"L. Santer, C. Bär, T. Thum","doi":"10.1016/j.ymthe.2019.07.001","DOIUrl":"https://doi.org/10.1016/j.ymthe.2019.07.001","url":null,"abstract":"","PeriodicalId":19039,"journal":{"name":"Molecular Therapy: the Journal of the American Society of Gene Therapy","volume":"63 1","pages":""},"PeriodicalIF":0.0,"publicationDate":"2019-08-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"83783902","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
引用次数: 148
Alliance of the Titans: An Effective Combination of a TKI with CAR T Cells. 泰坦联盟:TKI与CAR - T细胞的有效结合。
Pub Date : 2019-08-01 DOI: 10.1016/j.ymthe.2019.07.008
A. Heczey
{"title":"Alliance of the Titans: An Effective Combination of a TKI with CAR T Cells.","authors":"A. Heczey","doi":"10.1016/j.ymthe.2019.07.008","DOIUrl":"https://doi.org/10.1016/j.ymthe.2019.07.008","url":null,"abstract":"","PeriodicalId":19039,"journal":{"name":"Molecular Therapy: the Journal of the American Society of Gene Therapy","volume":"175 1","pages":""},"PeriodicalIF":0.0,"publicationDate":"2019-08-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"73167449","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
引用次数: 2
ASGCT Annual Meeting 2019. ASGCT 2019年年会。
Pub Date : 2019-07-18 DOI: 10.1016/j.ymthe.2019.07.004
S. Ylä-Herttuala
{"title":"ASGCT Annual Meeting 2019.","authors":"S. Ylä-Herttuala","doi":"10.1016/j.ymthe.2019.07.004","DOIUrl":"https://doi.org/10.1016/j.ymthe.2019.07.004","url":null,"abstract":"","PeriodicalId":19039,"journal":{"name":"Molecular Therapy: the Journal of the American Society of Gene Therapy","volume":"24 1","pages":""},"PeriodicalIF":0.0,"publicationDate":"2019-07-18","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"86072390","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
引用次数: 0
Family Highlights. 家庭的亮点。
Pub Date : 2019-06-01 DOI: 10.1016/j.ymthe.2019.05.010
{"title":"Family Highlights.","authors":"","doi":"10.1016/j.ymthe.2019.05.010","DOIUrl":"https://doi.org/10.1016/j.ymthe.2019.05.010","url":null,"abstract":"","PeriodicalId":19039,"journal":{"name":"Molecular Therapy: the Journal of the American Society of Gene Therapy","volume":"65 1","pages":"1232"},"PeriodicalIF":0.0,"publicationDate":"2019-06-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"80360959","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
引用次数: 1
Family Highlights. 家庭的亮点。
Pub Date : 2019-03-01 DOI: 10.1016/j.ymthe.2019.03.014
{"title":"Family Highlights.","authors":"","doi":"10.1016/j.ymthe.2019.03.014","DOIUrl":"https://doi.org/10.1016/j.ymthe.2019.03.014","url":null,"abstract":"","PeriodicalId":19039,"journal":{"name":"Molecular Therapy: the Journal of the American Society of Gene Therapy","volume":"71 1","pages":"2306"},"PeriodicalIF":0.0,"publicationDate":"2019-03-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"91532152","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
引用次数: 0
期刊
Molecular Therapy: the Journal of the American Society of Gene Therapy
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