Pub Date : 2017-03-01DOI: 10.1016/j.ymthe.2016.12.019
M. Flugelman, M. Halak, B. Yoffe, J. Schneiderman, Chen Rubinstein, A. Bloom, E. Weinmann, I. Goldin, V. Ginzburg, O. Mayzler, A. Hoffman, B. Koren, D. Gershtein, M. Inbar, Marina Hutoran, Adili Tsaba
{"title":"Phase Ib Safety, Two-Dose Study of MultiGeneAngio in Patients with Chronic Critical Limb Ischemia.","authors":"M. Flugelman, M. Halak, B. Yoffe, J. Schneiderman, Chen Rubinstein, A. Bloom, E. Weinmann, I. Goldin, V. Ginzburg, O. Mayzler, A. Hoffman, B. Koren, D. Gershtein, M. Inbar, Marina Hutoran, Adili Tsaba","doi":"10.1016/j.ymthe.2016.12.019","DOIUrl":"https://doi.org/10.1016/j.ymthe.2016.12.019","url":null,"abstract":"","PeriodicalId":19039,"journal":{"name":"Molecular Therapy: the Journal of the American Society of Gene Therapy","volume":"14 1","pages":"816-825"},"PeriodicalIF":0.0,"publicationDate":"2017-03-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"91145909","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
Pub Date : 2017-03-01DOI: 10.1016/j.ymthe.2016.12.025
H. Fu, Aaron S. Meadows, Tierra A Ware, R. Mohney, D. Mccarty
{"title":"Near-Complete Correction of Profound Metabolomic Impairments Corresponding to Functional Benefit in MPS IIIB Mice after IV rAAV9-hNAGLU Gene Delivery.","authors":"H. Fu, Aaron S. Meadows, Tierra A Ware, R. Mohney, D. Mccarty","doi":"10.1016/j.ymthe.2016.12.025","DOIUrl":"https://doi.org/10.1016/j.ymthe.2016.12.025","url":null,"abstract":"","PeriodicalId":19039,"journal":{"name":"Molecular Therapy: the Journal of the American Society of Gene Therapy","volume":"22 1","pages":"792-802"},"PeriodicalIF":0.0,"publicationDate":"2017-03-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"82031861","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
Pub Date : 2017-03-01DOI: 10.1016/j.ymthe.2017.02.002
S. Sahoo, P. Mathiyalagan, R. Hajjar
{"title":"Pericardial Fluid Exosomes: A New Material to Treat Cardiovascular Disease.","authors":"S. Sahoo, P. Mathiyalagan, R. Hajjar","doi":"10.1016/j.ymthe.2017.02.002","DOIUrl":"https://doi.org/10.1016/j.ymthe.2017.02.002","url":null,"abstract":"","PeriodicalId":19039,"journal":{"name":"Molecular Therapy: the Journal of the American Society of Gene Therapy","volume":"20 1","pages":"568-569"},"PeriodicalIF":0.0,"publicationDate":"2017-03-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"82095820","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
Pub Date : 2017-03-01DOI: 10.1016/j.ymthe.2016.12.023
Malika Hale, Taylor D. Mesojednik, G. S. Romano Ibarra, J. Sahni, Alison Bernard, Karen Sommer, A. Scharenberg, D. Rawlings, Thor A Wagner
{"title":"Engineering HIV-Resistant, Anti-HIV Chimeric Antigen Receptor T Cells.","authors":"Malika Hale, Taylor D. Mesojednik, G. S. Romano Ibarra, J. Sahni, Alison Bernard, Karen Sommer, A. Scharenberg, D. Rawlings, Thor A Wagner","doi":"10.1016/j.ymthe.2016.12.023","DOIUrl":"https://doi.org/10.1016/j.ymthe.2016.12.023","url":null,"abstract":"","PeriodicalId":19039,"journal":{"name":"Molecular Therapy: the Journal of the American Society of Gene Therapy","volume":"60 1","pages":"570-579"},"PeriodicalIF":0.0,"publicationDate":"2017-03-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"78733035","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
Pub Date : 2017-03-01DOI: 10.1016/j.ymthe.2016.12.017
Qian Zhang, Hong Ye, Fei-xiang Xiang, Lin-Jie Song, Li-Ling Zhou, P. Cai, Jian-chu Zhang, Fan Yu, Huanzhong Shi, Yunchao Su, J. Xin, Wan-Li Ma
{"title":"miR-18a-5p Inhibits Sub-pleural Pulmonary Fibrosis by Targeting TGF-β Receptor II.","authors":"Qian Zhang, Hong Ye, Fei-xiang Xiang, Lin-Jie Song, Li-Ling Zhou, P. Cai, Jian-chu Zhang, Fan Yu, Huanzhong Shi, Yunchao Su, J. Xin, Wan-Li Ma","doi":"10.1016/j.ymthe.2016.12.017","DOIUrl":"https://doi.org/10.1016/j.ymthe.2016.12.017","url":null,"abstract":"","PeriodicalId":19039,"journal":{"name":"Molecular Therapy: the Journal of the American Society of Gene Therapy","volume":"93 1","pages":"728-738"},"PeriodicalIF":0.0,"publicationDate":"2017-03-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"83863644","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
Pub Date : 2017-03-01DOI: 10.1016/j.ymthe.2017.01.018
Dan Liu, Hui Tang, Xinyan Li, Man-Fei Deng, N. Wei, Xiong Wang, Yafan Zhou, Ding-Qi Wang, Peng Fu, Jian-Zhi Wang, Sébastien S. Hébert, Jian-Guo Chen, Youming Lu, Ling-Qiang Zhu
{"title":"Targeting the HDAC2/HNF-4A/miR-101b/AMPK Pathway Rescues Tauopathy and Dendritic Abnormalities in Alzheimer's Disease.","authors":"Dan Liu, Hui Tang, Xinyan Li, Man-Fei Deng, N. Wei, Xiong Wang, Yafan Zhou, Ding-Qi Wang, Peng Fu, Jian-Zhi Wang, Sébastien S. Hébert, Jian-Guo Chen, Youming Lu, Ling-Qiang Zhu","doi":"10.1016/j.ymthe.2017.01.018","DOIUrl":"https://doi.org/10.1016/j.ymthe.2017.01.018","url":null,"abstract":"","PeriodicalId":19039,"journal":{"name":"Molecular Therapy: the Journal of the American Society of Gene Therapy","volume":"29 1","pages":"752-764"},"PeriodicalIF":0.0,"publicationDate":"2017-03-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"82299713","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
Pub Date : 2017-03-01DOI: 10.1016/j.ymthe.2016.12.024
K. Posey, F. Coustry, Alka C. Veerisetty, Mohammad G. Hossain, D. Gattis, S. Booten, J. Alcorn, P. Seth, J. Hecht
{"title":"Antisense Reduction of Mutant COMP Reduces Growth Plate Chondrocyte Pathology.","authors":"K. Posey, F. Coustry, Alka C. Veerisetty, Mohammad G. Hossain, D. Gattis, S. Booten, J. Alcorn, P. Seth, J. Hecht","doi":"10.1016/j.ymthe.2016.12.024","DOIUrl":"https://doi.org/10.1016/j.ymthe.2016.12.024","url":null,"abstract":"","PeriodicalId":19039,"journal":{"name":"Molecular Therapy: the Journal of the American Society of Gene Therapy","volume":"38 1","pages":"705-714"},"PeriodicalIF":0.0,"publicationDate":"2017-03-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"78419428","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
Pub Date : 2017-03-01DOI: 10.1016/j.ymthe.2016.12.009
Mao Mao, Liangli Wang, Chun-Chi Chang, Katheryn E. Rothenberg, Jianyong Huang, Yingxiao Wang, B. Hoffman, P. Liton, F. Yuan
{"title":"Involvement of a Rac1-Dependent Macropinocytosis Pathway in Plasmid DNA Delivery by Electrotransfection.","authors":"Mao Mao, Liangli Wang, Chun-Chi Chang, Katheryn E. Rothenberg, Jianyong Huang, Yingxiao Wang, B. Hoffman, P. Liton, F. Yuan","doi":"10.1016/j.ymthe.2016.12.009","DOIUrl":"https://doi.org/10.1016/j.ymthe.2016.12.009","url":null,"abstract":"","PeriodicalId":19039,"journal":{"name":"Molecular Therapy: the Journal of the American Society of Gene Therapy","volume":"96 1","pages":"803-815"},"PeriodicalIF":0.0,"publicationDate":"2017-03-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"90326402","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
Pub Date : 2017-03-01DOI: 10.1016/j.ymthe.2016.11.018
P. Duchesneau, R. Besla, M. Derouet, Li Guo, G. Karoubi, A. Silberberg, A. Wong, T. Waddell
{"title":"Partial Restoration of CFTR Function in cftr-Null Mice following Targeted Cell Replacement Therapy.","authors":"P. Duchesneau, R. Besla, M. Derouet, Li Guo, G. Karoubi, A. Silberberg, A. Wong, T. Waddell","doi":"10.1016/j.ymthe.2016.11.018","DOIUrl":"https://doi.org/10.1016/j.ymthe.2016.11.018","url":null,"abstract":"","PeriodicalId":19039,"journal":{"name":"Molecular Therapy: the Journal of the American Society of Gene Therapy","volume":"109 1","pages":"654-665"},"PeriodicalIF":0.0,"publicationDate":"2017-03-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"85721334","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
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