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Molecular Therapy: the Journal of the American Society of Gene Therapy最新文献

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Call for Papers: MT/MTNA Special Issue on mRNA Therapy. 关于mRNA治疗的MT/MTNA特刊征文。
Pub Date : 2018-01-01 DOI: 10.1016/j.ymthe.2018.05.010
R. Frederickson
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引用次数: 0
Orally Targeted Delivery of Tripeptide KPV via Hyaluronic Acid-Functionalized Nanoparticles Efficiently Alleviates Ulcerative Colitis. 通过透明质酸功能化纳米颗粒口服靶向递送三肽KPV有效缓解溃疡性结肠炎。
Pub Date : 2017-07-05 DOI: 10.1016/j.ymthe.2016.11.020
Bo Xiao, Zhigang Xu, É. Viennois, Yuchen Zhang, Zhan Zhang, Mingzhen Zhang, Moon K Han, Yuejun Kang, D. Merlin
{"title":"Orally Targeted Delivery of Tripeptide KPV via Hyaluronic Acid-Functionalized Nanoparticles Efficiently Alleviates Ulcerative Colitis.","authors":"Bo Xiao, Zhigang Xu, É. Viennois, Yuchen Zhang, Zhan Zhang, Mingzhen Zhang, Moon K Han, Yuejun Kang, D. Merlin","doi":"10.1016/j.ymthe.2016.11.020","DOIUrl":"https://doi.org/10.1016/j.ymthe.2016.11.020","url":null,"abstract":"","PeriodicalId":19039,"journal":{"name":"Molecular Therapy: the Journal of the American Society of Gene Therapy","volume":"94 1","pages":"1628-1640"},"PeriodicalIF":0.0,"publicationDate":"2017-07-05","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"90274795","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
引用次数: 126
RNA Nanoparticle-Based Targeted Therapy for Glioblastoma through Inhibition of Oncogenic miR-21. RNA纳米颗粒通过抑制致癌miR-21靶向治疗胶质母细胞瘤。
Pub Date : 2017-07-05 DOI: 10.1016/j.ymthe.2016.11.016
T. Lee, J. Yoo, Dan Shu, Hui Li, Jianying Zhang, Jun‐ge Yu, A. C. Jaime-Ramirez, M. Acunzo, G. Romano, R. Cui, Hui-Lung Sun, Zhenghua Luo, M. Old, B. Kaur, Peixuan Guo, C. Croce
{"title":"RNA Nanoparticle-Based Targeted Therapy for Glioblastoma through Inhibition of Oncogenic miR-21.","authors":"T. Lee, J. Yoo, Dan Shu, Hui Li, Jianying Zhang, Jun‐ge Yu, A. C. Jaime-Ramirez, M. Acunzo, G. Romano, R. Cui, Hui-Lung Sun, Zhenghua Luo, M. Old, B. Kaur, Peixuan Guo, C. Croce","doi":"10.1016/j.ymthe.2016.11.016","DOIUrl":"https://doi.org/10.1016/j.ymthe.2016.11.016","url":null,"abstract":"","PeriodicalId":19039,"journal":{"name":"Molecular Therapy: the Journal of the American Society of Gene Therapy","volume":"31 1","pages":"1544-1555"},"PeriodicalIF":0.0,"publicationDate":"2017-07-05","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"80791239","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
引用次数: 104
Viral Vector Reprogramming of Adult Resident Striatal Oligodendrocytes into Functional Neurons. 成年纹状体少突胶质细胞成功能神经元的病毒载体重编程。
Pub Date : 2017-04-05 DOI: 10.1016/j.ymthe.2017.01.016
M. Weinberg, H. Criswell, S. Powell, A. Bhatt, T. McCown
{"title":"Viral Vector Reprogramming of Adult Resident Striatal Oligodendrocytes into Functional Neurons.","authors":"M. Weinberg, H. Criswell, S. Powell, A. Bhatt, T. McCown","doi":"10.1016/j.ymthe.2017.01.016","DOIUrl":"https://doi.org/10.1016/j.ymthe.2017.01.016","url":null,"abstract":"","PeriodicalId":19039,"journal":{"name":"Molecular Therapy: the Journal of the American Society of Gene Therapy","volume":"12 1","pages":"928-934"},"PeriodicalIF":0.0,"publicationDate":"2017-04-05","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"83465592","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
引用次数: 39
Safe Recombinant Outer Membrane Vesicles that Display M2e Elicit Heterologous Influenza Protection. 显示M2e的安全重组外膜囊泡引发异源流感保护。
Pub Date : 2017-04-05 DOI: 10.1016/j.ymthe.2017.01.010
H. Watkins, C. G. Rappazzo, Jaclyn Higgins, Xiangjie Sun, N. Brock, Annie Chau, Aditya Misra, Joseph P B Cannizzo, M. King, T. Maines, C. Leifer, G. Whittaker, M. DeLisa, D. Putnam
{"title":"Safe Recombinant Outer Membrane Vesicles that Display M2e Elicit Heterologous Influenza Protection.","authors":"H. Watkins, C. G. Rappazzo, Jaclyn Higgins, Xiangjie Sun, N. Brock, Annie Chau, Aditya Misra, Joseph P B Cannizzo, M. King, T. Maines, C. Leifer, G. Whittaker, M. DeLisa, D. Putnam","doi":"10.1016/j.ymthe.2017.01.010","DOIUrl":"https://doi.org/10.1016/j.ymthe.2017.01.010","url":null,"abstract":"","PeriodicalId":19039,"journal":{"name":"Molecular Therapy: the Journal of the American Society of Gene Therapy","volume":"164 1","pages":"989-1002"},"PeriodicalIF":0.0,"publicationDate":"2017-04-05","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"74494865","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
引用次数: 68
HIV Receives a "One Two Knockout Punch". 艾滋病病毒受到了“一拳两击”。
Pub Date : 2017-03-01 DOI: 10.1016/j.ymthe.2017.02.001
C. Cruz, C. Bollard
{"title":"HIV Receives a \"One Two Knockout Punch\".","authors":"C. Cruz, C. Bollard","doi":"10.1016/j.ymthe.2017.02.001","DOIUrl":"https://doi.org/10.1016/j.ymthe.2017.02.001","url":null,"abstract":"","PeriodicalId":19039,"journal":{"name":"Molecular Therapy: the Journal of the American Society of Gene Therapy","volume":"44 1","pages":"566-567"},"PeriodicalIF":0.0,"publicationDate":"2017-03-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"86554169","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
引用次数: 0
Lentiviral Transfer of γ-Globin with Fusion Gene NUP98-HOXA10HD Expands Hematopoietic Stem Cells and Ameliorates Murine β-Thalassemia. 融合基因NUP98-HOXA10HD的γ-珠蛋白慢病毒转移扩增造血干细胞并改善小鼠β-地中海贫血
Pub Date : 2017-03-01 DOI: 10.1016/j.ymthe.2017.01.019
Huifen Zhao, Allistair A. Abraham, Yoon-Sang Kim, Yong-Dong Wang, T. Pestina, J. Zhan, K. Humphries, A. Nienhuis, D. Persons
{"title":"Lentiviral Transfer of γ-Globin with Fusion Gene NUP98-HOXA10HD Expands Hematopoietic Stem Cells and Ameliorates Murine β-Thalassemia.","authors":"Huifen Zhao, Allistair A. Abraham, Yoon-Sang Kim, Yong-Dong Wang, T. Pestina, J. Zhan, K. Humphries, A. Nienhuis, D. Persons","doi":"10.1016/j.ymthe.2017.01.019","DOIUrl":"https://doi.org/10.1016/j.ymthe.2017.01.019","url":null,"abstract":"","PeriodicalId":19039,"journal":{"name":"Molecular Therapy: the Journal of the American Society of Gene Therapy","volume":"42 1","pages":"593-605"},"PeriodicalIF":0.0,"publicationDate":"2017-03-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"91375292","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
引用次数: 7
Genome Editing for Sickle Cell Disease: A Little BCL11A Goes a Long Way. 镰状细胞病的基因组编辑:一点BCL11A大有帮助。
Pub Date : 2017-03-01 DOI: 10.1016/j.ymthe.2017.02.003
Mir A. Hossain, J. Bungert
{"title":"Genome Editing for Sickle Cell Disease: A Little BCL11A Goes a Long Way.","authors":"Mir A. Hossain, J. Bungert","doi":"10.1016/j.ymthe.2017.02.003","DOIUrl":"https://doi.org/10.1016/j.ymthe.2017.02.003","url":null,"abstract":"","PeriodicalId":19039,"journal":{"name":"Molecular Therapy: the Journal of the American Society of Gene Therapy","volume":"22 1","pages":"561-562"},"PeriodicalIF":0.0,"publicationDate":"2017-03-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"73532665","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
引用次数: 8
Intra-articular Delivery of Antago-miR-483-5p Inhibits Osteoarthritis by Modulating Matrilin 3 and Tissue Inhibitor of Metalloproteinase 2. Antago-miR-483-5p关节内递送通过调节基质蛋白3和金属蛋白酶2组织抑制剂抑制骨关节炎。
Pub Date : 2017-03-01 DOI: 10.1016/j.ymthe.2016.12.020
Hua Wang, Haiyan Zhang, Qiuyi Sun, Yun Wang, Jun Yang, Jincheng Yang, Tao Zhang, S. Luo, Liping Wang, Yu Jiang, C. Zeng, D. Cai, X. Bai
{"title":"Intra-articular Delivery of Antago-miR-483-5p Inhibits Osteoarthritis by Modulating Matrilin 3 and Tissue Inhibitor of Metalloproteinase 2.","authors":"Hua Wang, Haiyan Zhang, Qiuyi Sun, Yun Wang, Jun Yang, Jincheng Yang, Tao Zhang, S. Luo, Liping Wang, Yu Jiang, C. Zeng, D. Cai, X. Bai","doi":"10.1016/j.ymthe.2016.12.020","DOIUrl":"https://doi.org/10.1016/j.ymthe.2016.12.020","url":null,"abstract":"","PeriodicalId":19039,"journal":{"name":"Molecular Therapy: the Journal of the American Society of Gene Therapy","volume":"58 1","pages":"715-727"},"PeriodicalIF":0.0,"publicationDate":"2017-03-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"83125130","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
引用次数: 69
Phase Ib Safety, Two-Dose Study of MultiGeneAngio in Patients with Chronic Critical Limb Ischemia. 多基因血管治疗慢性重度肢体缺血的Ib期安全性、双剂量研究。
Pub Date : 2017-03-01 DOI: 10.1016/j.ymthe.2016.12.019
M. Flugelman, M. Halak, B. Yoffe, J. Schneiderman, Chen Rubinstein, A. Bloom, E. Weinmann, I. Goldin, V. Ginzburg, O. Mayzler, A. Hoffman, B. Koren, D. Gershtein, M. Inbar, Marina Hutoran, Adili Tsaba
{"title":"Phase Ib Safety, Two-Dose Study of MultiGeneAngio in Patients with Chronic Critical Limb Ischemia.","authors":"M. Flugelman, M. Halak, B. Yoffe, J. Schneiderman, Chen Rubinstein, A. Bloom, E. Weinmann, I. Goldin, V. Ginzburg, O. Mayzler, A. Hoffman, B. Koren, D. Gershtein, M. Inbar, Marina Hutoran, Adili Tsaba","doi":"10.1016/j.ymthe.2016.12.019","DOIUrl":"https://doi.org/10.1016/j.ymthe.2016.12.019","url":null,"abstract":"","PeriodicalId":19039,"journal":{"name":"Molecular Therapy: the Journal of the American Society of Gene Therapy","volume":"14 1","pages":"816-825"},"PeriodicalIF":0.0,"publicationDate":"2017-03-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"91145909","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
引用次数: 16
期刊
Molecular Therapy: the Journal of the American Society of Gene Therapy
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