Pub Date : 2018-01-01DOI: 10.1016/j.ymthe.2018.05.010
R. Frederickson
{"title":"Call for Papers: MT/MTNA Special Issue on mRNA Therapy.","authors":"R. Frederickson","doi":"10.1016/j.ymthe.2018.05.010","DOIUrl":"https://doi.org/10.1016/j.ymthe.2018.05.010","url":null,"abstract":"","PeriodicalId":19039,"journal":{"name":"Molecular Therapy: the Journal of the American Society of Gene Therapy","volume":"16 1","pages":"1395"},"PeriodicalIF":0.0,"publicationDate":"2018-01-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"88543501","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
Pub Date : 2017-07-05DOI: 10.1016/j.ymthe.2016.11.020
Bo Xiao, Zhigang Xu, É. Viennois, Yuchen Zhang, Zhan Zhang, Mingzhen Zhang, Moon K Han, Yuejun Kang, D. Merlin
{"title":"Orally Targeted Delivery of Tripeptide KPV via Hyaluronic Acid-Functionalized Nanoparticles Efficiently Alleviates Ulcerative Colitis.","authors":"Bo Xiao, Zhigang Xu, É. Viennois, Yuchen Zhang, Zhan Zhang, Mingzhen Zhang, Moon K Han, Yuejun Kang, D. Merlin","doi":"10.1016/j.ymthe.2016.11.020","DOIUrl":"https://doi.org/10.1016/j.ymthe.2016.11.020","url":null,"abstract":"","PeriodicalId":19039,"journal":{"name":"Molecular Therapy: the Journal of the American Society of Gene Therapy","volume":"94 1","pages":"1628-1640"},"PeriodicalIF":0.0,"publicationDate":"2017-07-05","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"90274795","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
Pub Date : 2017-07-05DOI: 10.1016/j.ymthe.2016.11.016
T. Lee, J. Yoo, Dan Shu, Hui Li, Jianying Zhang, Jun‐ge Yu, A. C. Jaime-Ramirez, M. Acunzo, G. Romano, R. Cui, Hui-Lung Sun, Zhenghua Luo, M. Old, B. Kaur, Peixuan Guo, C. Croce
{"title":"RNA Nanoparticle-Based Targeted Therapy for Glioblastoma through Inhibition of Oncogenic miR-21.","authors":"T. Lee, J. Yoo, Dan Shu, Hui Li, Jianying Zhang, Jun‐ge Yu, A. C. Jaime-Ramirez, M. Acunzo, G. Romano, R. Cui, Hui-Lung Sun, Zhenghua Luo, M. Old, B. Kaur, Peixuan Guo, C. Croce","doi":"10.1016/j.ymthe.2016.11.016","DOIUrl":"https://doi.org/10.1016/j.ymthe.2016.11.016","url":null,"abstract":"","PeriodicalId":19039,"journal":{"name":"Molecular Therapy: the Journal of the American Society of Gene Therapy","volume":"31 1","pages":"1544-1555"},"PeriodicalIF":0.0,"publicationDate":"2017-07-05","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"80791239","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
Pub Date : 2017-04-05DOI: 10.1016/j.ymthe.2017.01.016
M. Weinberg, H. Criswell, S. Powell, A. Bhatt, T. McCown
{"title":"Viral Vector Reprogramming of Adult Resident Striatal Oligodendrocytes into Functional Neurons.","authors":"M. Weinberg, H. Criswell, S. Powell, A. Bhatt, T. McCown","doi":"10.1016/j.ymthe.2017.01.016","DOIUrl":"https://doi.org/10.1016/j.ymthe.2017.01.016","url":null,"abstract":"","PeriodicalId":19039,"journal":{"name":"Molecular Therapy: the Journal of the American Society of Gene Therapy","volume":"12 1","pages":"928-934"},"PeriodicalIF":0.0,"publicationDate":"2017-04-05","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"83465592","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
Pub Date : 2017-04-05DOI: 10.1016/j.ymthe.2017.01.010
H. Watkins, C. G. Rappazzo, Jaclyn Higgins, Xiangjie Sun, N. Brock, Annie Chau, Aditya Misra, Joseph P B Cannizzo, M. King, T. Maines, C. Leifer, G. Whittaker, M. DeLisa, D. Putnam
{"title":"Safe Recombinant Outer Membrane Vesicles that Display M2e Elicit Heterologous Influenza Protection.","authors":"H. Watkins, C. G. Rappazzo, Jaclyn Higgins, Xiangjie Sun, N. Brock, Annie Chau, Aditya Misra, Joseph P B Cannizzo, M. King, T. Maines, C. Leifer, G. Whittaker, M. DeLisa, D. Putnam","doi":"10.1016/j.ymthe.2017.01.010","DOIUrl":"https://doi.org/10.1016/j.ymthe.2017.01.010","url":null,"abstract":"","PeriodicalId":19039,"journal":{"name":"Molecular Therapy: the Journal of the American Society of Gene Therapy","volume":"164 1","pages":"989-1002"},"PeriodicalIF":0.0,"publicationDate":"2017-04-05","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"74494865","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
Pub Date : 2017-03-01DOI: 10.1016/j.ymthe.2017.02.001
C. Cruz, C. Bollard
{"title":"HIV Receives a \"One Two Knockout Punch\".","authors":"C. Cruz, C. Bollard","doi":"10.1016/j.ymthe.2017.02.001","DOIUrl":"https://doi.org/10.1016/j.ymthe.2017.02.001","url":null,"abstract":"","PeriodicalId":19039,"journal":{"name":"Molecular Therapy: the Journal of the American Society of Gene Therapy","volume":"44 1","pages":"566-567"},"PeriodicalIF":0.0,"publicationDate":"2017-03-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"86554169","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
Pub Date : 2017-03-01DOI: 10.1016/j.ymthe.2017.01.019
Huifen Zhao, Allistair A. Abraham, Yoon-Sang Kim, Yong-Dong Wang, T. Pestina, J. Zhan, K. Humphries, A. Nienhuis, D. Persons
{"title":"Lentiviral Transfer of γ-Globin with Fusion Gene NUP98-HOXA10HD Expands Hematopoietic Stem Cells and Ameliorates Murine β-Thalassemia.","authors":"Huifen Zhao, Allistair A. Abraham, Yoon-Sang Kim, Yong-Dong Wang, T. Pestina, J. Zhan, K. Humphries, A. Nienhuis, D. Persons","doi":"10.1016/j.ymthe.2017.01.019","DOIUrl":"https://doi.org/10.1016/j.ymthe.2017.01.019","url":null,"abstract":"","PeriodicalId":19039,"journal":{"name":"Molecular Therapy: the Journal of the American Society of Gene Therapy","volume":"42 1","pages":"593-605"},"PeriodicalIF":0.0,"publicationDate":"2017-03-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"91375292","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
Pub Date : 2017-03-01DOI: 10.1016/j.ymthe.2017.02.003
Mir A. Hossain, J. Bungert
{"title":"Genome Editing for Sickle Cell Disease: A Little BCL11A Goes a Long Way.","authors":"Mir A. Hossain, J. Bungert","doi":"10.1016/j.ymthe.2017.02.003","DOIUrl":"https://doi.org/10.1016/j.ymthe.2017.02.003","url":null,"abstract":"","PeriodicalId":19039,"journal":{"name":"Molecular Therapy: the Journal of the American Society of Gene Therapy","volume":"22 1","pages":"561-562"},"PeriodicalIF":0.0,"publicationDate":"2017-03-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"73532665","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
Pub Date : 2017-03-01DOI: 10.1016/j.ymthe.2016.12.020
Hua Wang, Haiyan Zhang, Qiuyi Sun, Yun Wang, Jun Yang, Jincheng Yang, Tao Zhang, S. Luo, Liping Wang, Yu Jiang, C. Zeng, D. Cai, X. Bai
{"title":"Intra-articular Delivery of Antago-miR-483-5p Inhibits Osteoarthritis by Modulating Matrilin 3 and Tissue Inhibitor of Metalloproteinase 2.","authors":"Hua Wang, Haiyan Zhang, Qiuyi Sun, Yun Wang, Jun Yang, Jincheng Yang, Tao Zhang, S. Luo, Liping Wang, Yu Jiang, C. Zeng, D. Cai, X. Bai","doi":"10.1016/j.ymthe.2016.12.020","DOIUrl":"https://doi.org/10.1016/j.ymthe.2016.12.020","url":null,"abstract":"","PeriodicalId":19039,"journal":{"name":"Molecular Therapy: the Journal of the American Society of Gene Therapy","volume":"58 1","pages":"715-727"},"PeriodicalIF":0.0,"publicationDate":"2017-03-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"83125130","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
Pub Date : 2017-03-01DOI: 10.1016/j.ymthe.2016.12.019
M. Flugelman, M. Halak, B. Yoffe, J. Schneiderman, Chen Rubinstein, A. Bloom, E. Weinmann, I. Goldin, V. Ginzburg, O. Mayzler, A. Hoffman, B. Koren, D. Gershtein, M. Inbar, Marina Hutoran, Adili Tsaba
{"title":"Phase Ib Safety, Two-Dose Study of MultiGeneAngio in Patients with Chronic Critical Limb Ischemia.","authors":"M. Flugelman, M. Halak, B. Yoffe, J. Schneiderman, Chen Rubinstein, A. Bloom, E. Weinmann, I. Goldin, V. Ginzburg, O. Mayzler, A. Hoffman, B. Koren, D. Gershtein, M. Inbar, Marina Hutoran, Adili Tsaba","doi":"10.1016/j.ymthe.2016.12.019","DOIUrl":"https://doi.org/10.1016/j.ymthe.2016.12.019","url":null,"abstract":"","PeriodicalId":19039,"journal":{"name":"Molecular Therapy: the Journal of the American Society of Gene Therapy","volume":"14 1","pages":"816-825"},"PeriodicalIF":0.0,"publicationDate":"2017-03-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"91145909","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}